Perspectives on Spinraza (Nusinersen) Treatment Study: Views of Individuals and Parents of Children Diagnosed with Spinal Muscular Atrophy.
J Neuromuscul Dis
; 6(1): 119-131, 2019.
Article
in En
| MEDLINE
| ID: mdl-30594933
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Oligonucleotides
/
Muscular Atrophy, Spinal
Type of study:
Diagnostic_studies
/
Etiology_studies
/
Prognostic_studies
/
Qualitative_research
Aspects:
Patient_preference
Limits:
Adult
/
Female
/
Humans
/
Male
/
Middle aged
Language:
En
Journal:
J Neuromuscul Dis
Year:
2019
Document type:
Article
Affiliation country:
United States
Country of publication:
Netherlands