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Hematopoietic stem cell transplantation for CD40 ligand deficiency: Results from an EBMT/ESID-IEWP-SCETIDE-PIDTC study.
Ferrua, Francesca; Galimberti, Stefania; Courteille, Virginie; Slatter, Mary Anne; Booth, Claire; Moshous, Despina; Neven, Benedicte; Blanche, Stephane; Cavazzana, Marina; Laberko, Alexandra; Shcherbina, Anna; Balashov, Dmitry; Soncini, Elena; Porta, Fulvio; Al-Mousa, Hamoud; Al-Saud, Bandar; Al-Dhekri, Hasan; Arnaout, Rand; Formankova, Renata; Bertrand, Yves; Lange, Andrzej; Smart, Joanne; Wolska-Kusnierz, Beata; Aquino, Victor M; Dvorak, Christopher C; Fasth, Anders; Fouyssac, Fanny; Heilmann, Carsten; Hoenig, Manfred; Schuetz, Catharina; Kelecic, Jadranka; Bredius, Robbert G M; Lankester, Arjan C; Lindemans, Caroline A; Suarez, Felipe; Sullivan, Kathleen E; Albert, Michael H; Kalwak, Krzysztof; Barlogis, Vincent; Bhatia, Monica; Bordon, Victoria; Czogala, Wojciech; Alonso, Laura; Dogu, Figen; Gozdzik, Jolanta; Ikinciogullari, Aydan; Kriván, Gergely; Ljungman, Per; Meyts, Isabelle; Mustillo, Peter.
Affiliation
  • Ferrua F; Department of Pediatric Immunology and HSCT, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom; San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Pediatric Immunohematology and Bone Marrow Transplantation Unit, San Raffaele Scientific Institute, Milan, Italy; Vita-Salut
  • Galimberti S; Center of Biostatistics for Clinical Epidemiology, School of Medicine and Surgery, University of Milano-Bicocca, Monza, Italy.
  • Courteille V; Paris Descartes-Sorbonne Paris Cité University, Imagine Institute, Paris, France; French National Reference Center for Primary Immune Deficiencies (CEREDIH), Necker Enfants Malades University Hospital, AP-HP, Paris, France.
  • Slatter MA; Department of Pediatric Immunology and HSCT, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom; Institute of Cellular Medicine, Newcastle University, Newcastle upon Tyne, United Kingdom.
  • Booth C; Department of Pediatric Immunology, Great Ormond Street Hospital, London, United Kingdom.
  • Moshous D; Paris Descartes-Sorbonne Paris Cité University, Imagine Institute, Paris, France; Pediatric Hematology-Immunology and Rheumatology Unit, Necker-Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France; French National Reference Center for Primary Immune Deficiencies (CE
  • Neven B; Paris Descartes-Sorbonne Paris Cité University, Imagine Institute, Paris, France; Pediatric Hematology-Immunology and Rheumatology Unit, Necker-Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France; French National Reference Center for Primary Immune Deficiencies (CE
  • Blanche S; Paris Descartes-Sorbonne Paris Cité University, Imagine Institute, Paris, France; Pediatric Hematology-Immunology and Rheumatology Unit, Necker-Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France; French National Reference Center for Primary Immune Deficiencies (CE
  • Cavazzana M; Paris Descartes-Sorbonne Paris Cité University, Imagine Institute, Paris, France; Biotherapy Department, Necker Children's Hospital, AP-HP, Paris, France; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, AP-HP, INSERM, Paris, France; INSERM UMR 1163, Laboratory of Hu
  • Laberko A; Dmitry Rogachev Federal Research Centre of Pediatric Hematology, Oncology and Immunology, Moscow, Russia.
  • Shcherbina A; Dmitry Rogachev Federal Research Centre of Pediatric Hematology, Oncology and Immunology, Moscow, Russia.
  • Balashov D; Dmitry Rogachev Federal Research Centre of Pediatric Hematology, Oncology and Immunology, Moscow, Russia.
  • Soncini E; Pediatric Oncology-Hematology and BMT Unit, Spedali Civili di Brescia, Brescia, Italy.
  • Porta F; Pediatric Oncology-Hematology and BMT Unit, Spedali Civili di Brescia, Brescia, Italy.
  • Al-Mousa H; Department of Pediatrics, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia.
  • Al-Saud B; Department of Pediatrics, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia.
  • Al-Dhekri H; Department of Pediatrics, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia.
  • Arnaout R; Department of Pediatrics, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia.
  • Formankova R; Department of Pediatric Hematology and Oncology, University Hospital Motol Prague, Prague, Czech Republic.
  • Bertrand Y; Institut d'Hematologie et d'Oncologie Pediatrique, Hospices Civils de Lyon, Lyon, France.
  • Lange A; L. Hirszfeld Institute of Immunology and Experimental Therapy, Polish Academy of Sciences, Wroclaw, Poland; Lower Silesian Center for Cellular Transplantation & National Bone Marrow Donor Registry, Wroclaw, Poland.
  • Smart J; Department of Allergy and Immunology, Royal Children's Hospital, Melbourne, Australia.
  • Wolska-Kusnierz B; Immunology Department, Children's Memorial Health Institute, Warsaw, Poland.
  • Aquino VM; Department of Pediatrics, University of Texas Southwestern Medical Center Dallas, Dallas, Tex.
  • Dvorak CC; Division of Pediatric Allergy, Immunology & Bone Marrow Transplantation, University of California, San Francisco, Calif.
  • Fasth A; Department of Pediatrics, Sahlgrenska Academy at University of Gothenburg and Queen Silvia Children's Hospital, Gothenburg, Sweden.
  • Fouyssac F; Pediatric Oncology and Hematology Unit, Children Hospital, University Hospital Nancy, Vandoeuvre-les-Nancy, France; French National Reference Center for Primary Immune Deficiencies (CEREDIH), Necker Enfants Malades University Hospital, AP-HP, Paris, France.
  • Heilmann C; Pediatric Clinic, Rigshospitalet, Copenhagen, Denmark.
  • Hoenig M; Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
  • Schuetz C; Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
  • Kelecic J; Department of Pediatrics, Division of Allergology, Clinical Immunology, Respiratory Diseases and Rheumatology, University Hospital Center Zagreb, Zagreb, Croatia.
  • Bredius RGM; Department of Pediatrics/Willem-Alexander Children's hospital, Leiden University Medical Center, Leiden, The Netherlands.
  • Lankester AC; Department of Pediatrics/Willem-Alexander Children's hospital, Leiden University Medical Center, Leiden, The Netherlands.
  • Lindemans CA; Department of Pediatrics, University Medical Centre Utrecht, Utrecht University, Utrecht, The Netherlands; Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.
  • Suarez F; Hématologie Adulte, Hôpital Necker, AP-HP, Paris, France; French National Reference Center for Primary Immune Deficiencies (CEREDIH), Necker Enfants Malades University Hospital, AP-HP, Paris, France.
  • Sullivan KE; Division of Allergy Immunology, Department of Pediatrics, Children's Hospital of Philadelphia, Philadelphia, Pa.
  • Albert MH; Pediatric Hematology/Oncology, Dr. von Hauner University Children's Hospital, Munich, Germany.
  • Kalwak K; Department of Pediatric Hematology and Oncology, Wroclaw Medical University, Wroclaw, Poland.
  • Barlogis V; Service d'hématologie pédiatrique, Hôpital de la Timone Enfants, Marseille, France; French National Reference Center for Primary Immune Deficiencies (CEREDIH), Necker Enfants Malades University Hospital, AP-HP, Paris, France.
  • Bhatia M; Pediatric Stem Cell Transplantation, Columbia University College of Physicians and Surgeons, New York, NY.
  • Bordon V; Pediatric Hematology-Oncology and Stem Cell Transplantation, Ghent University Hospital, Ghent, Belgium.
  • Czogala W; University Children's Hospital of Cracow, Cracow, Poland.
  • Alonso L; Pediatric Hematology and Oncology Department, Hospital Universitario MaternoInfantil Vall d'Hebron, Barcelona, Spain.
  • Dogu F; Department of Pediatric Immunology and Allergy, Ankara University School of Medicine, Ankara, Turkey.
  • Gozdzik J; Department of Clinical Immunology and Transplantology, Jagiellonian University, Medical Collage, Transplantation Center, University Children's Hospital, Cracow, Poland.
  • Ikinciogullari A; Department of Pediatric Immunology-Allergy and BMT Unit, Ankara University Medical School, Ankara, Turkey.
  • Kriván G; Department of Pediatric Hematology and Stem Cell Transplantation United St. István and St László Hospital, Budapest, Hungary.
  • Ljungman P; Department of Hematology, Karolinska University Hospital, Stockholm, Sweden.
  • Meyts I; Department of Pediatrics, University Hospitals Leuven, Division of Pediatric Immunology, Department of Immunology and Microbiology, Catholic University Leuven, Leuven, Belgium.
  • Mustillo P; Nationwide Children's Hospital, Columbus, Ohio.
J Allergy Clin Immunol ; 143(6): 2238-2253, 2019 06.
Article in En | MEDLINE | ID: mdl-30660643

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hematopoietic Stem Cell Transplantation / CD40 Ligand / X-Linked Combined Immunodeficiency Diseases Type of study: Observational_studies / Risk_factors_studies Limits: Child / Child, preschool / Humans / Infant / Newborn Language: En Journal: J Allergy Clin Immunol Year: 2019 Document type: Article Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hematopoietic Stem Cell Transplantation / CD40 Ligand / X-Linked Combined Immunodeficiency Diseases Type of study: Observational_studies / Risk_factors_studies Limits: Child / Child, preschool / Humans / Infant / Newborn Language: En Journal: J Allergy Clin Immunol Year: 2019 Document type: Article Country of publication: United States