Innovative Curative Treatment of Beta Thalassemia: Cost-Efficacy Analysis of Gene Therapy Versus Allogenic Hematopoietic Stem-Cell Transplantation.
Hum Gene Ther
; 30(6): 753-761, 2019 06.
Article
in En
| MEDLINE
| ID: mdl-30700149
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Genetic Therapy
/
Beta-Thalassemia
/
Hematopoietic Stem Cell Transplantation
Type of study:
Diagnostic_studies
/
Etiology_studies
/
Health_economic_evaluation
/
Observational_studies
/
Prognostic_studies
Limits:
Adolescent
/
Child
/
Child, preschool
/
Humans
/
Infant
Language:
En
Journal:
Hum Gene Ther
Journal subject:
GENETICA MEDICA
/
TERAPEUTICA
Year:
2019
Document type:
Article
Affiliation country:
France
Country of publication:
United States