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Advances and challenges for hemophilia gene therapy.
Batty, Paul; Lillicrap, David.
Affiliation
  • Batty P; Department of Pathology and Molecular Medicine, Richardson Laboratory, Queen's University, Kingston, Ontario, Canada.
  • Lillicrap D; Department of Pathology and Molecular Medicine, Richardson Laboratory, Queen's University, Kingston, Ontario, Canada.
Hum Mol Genet ; 28(R1): R95-R101, 2019 10 01.
Article in En | MEDLINE | ID: mdl-31332444

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor IX / Factor VIII / Genetic Therapy / Hemophilia B / Hemophilia A Type of study: Prognostic_studies Aspects: Patient_preference Limits: Animals / Humans Language: En Journal: Hum Mol Genet Journal subject: BIOLOGIA MOLECULAR / GENETICA MEDICA Year: 2019 Document type: Article Affiliation country: Canada

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor IX / Factor VIII / Genetic Therapy / Hemophilia B / Hemophilia A Type of study: Prognostic_studies Aspects: Patient_preference Limits: Animals / Humans Language: En Journal: Hum Mol Genet Journal subject: BIOLOGIA MOLECULAR / GENETICA MEDICA Year: 2019 Document type: Article Affiliation country: Canada