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Correction of Glycogen Synthase Kinase 3ß in Myotonic Dystrophy 1 Reduces the Mutant RNA and Improves Postnatal Survival of DMSXL Mice.
Wang, Mei; Weng, Wen-Chin; Stock, Lauren; Lindquist, Diana; Martinez, Ana; Gourdon, Genevieve; Timchenko, Nikolai; Snape, Mike; Timchenko, Lubov.
Affiliation
  • Wang M; Division of Neurology, Cincinnati Children's Hospital, Cincinnati, Ohio, USA.
  • Weng WC; Division of Neurology, Cincinnati Children's Hospital, Cincinnati, Ohio, USA.
  • Stock L; Division of Neurology, Cincinnati Children's Hospital, Cincinnati, Ohio, USA.
  • Lindquist D; Imaging Research Center, Cincinnati Children's Hospital, Cincinnati, Ohio, USA.
  • Martinez A; Centro de Investigaciones Biológicas (CIB, CSIC), Madrid, Spain.
  • Gourdon G; Inserm UMR1163, Institut Imagine, Université Paris Descartes-Sorbonne Paris Cité, Paris, France.
  • Timchenko N; Departments of Surgery, Cincinnati Children's Hospital, University of Cincinnati, College of Medicine, Cincinnati, Ohio, USA.
  • Snape M; Departments of Pediatrics, University of Cincinnati, College of Medicine, Cincinnati, Ohio, USA.
  • Timchenko L; AMO Pharma Ltd., Wonersh, Surrey, United Kingdom.
Mol Cell Biol ; 39(21)2019 11 01.
Article in En | MEDLINE | ID: mdl-31383751

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Synthase Kinase 3 beta / Myotonic Dystrophy Type of study: Prognostic_studies Limits: Animals / Humans Language: En Journal: Mol Cell Biol Year: 2019 Document type: Article Affiliation country: United States Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Synthase Kinase 3 beta / Myotonic Dystrophy Type of study: Prognostic_studies Limits: Animals / Humans Language: En Journal: Mol Cell Biol Year: 2019 Document type: Article Affiliation country: United States Country of publication: United States