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Haemophilia A: health and economic burden of a rare disease in Portugal.
Café, Andreia; Carvalho, Manuela; Crato, Miguel; Faria, Miguel; Kjollerstrom, Paula; Oliveira, Cristina; Pinto, Patrícia R; Salvado, Ramón; Dos Santos, Alexandra Aires; Silva, Catarina.
Affiliation
  • Café A; Market Access & External Affairs, Roche Farmacêutica Química, Lda, Estrada Nacional 249 - 1, 2720-413, Amadora, Portugal. andreia.cafe@roche.com.
  • Carvalho M; Centro de Referência de Coagulopatias Congénitas do Centro Hospitalar Universitário S. João, EPE, Porto, Portugal.
  • Crato M; Associação Portuguesa de Hemofilia e de Outras Coagulopatias Congénitas, Lisbon, Portugal.
  • Faria M; Health Economics, Eurotrials Scientific Consultants, now part of CTI Clinical Trial & Consulting Services, Lisbon, Portugal.
  • Kjollerstrom P; Unidade de Hematologia Pediátrica, Hospital Dona Estefânia, Centro Hospitalar Lisboa Central, Lisbon, Portugal.
  • Oliveira C; Centro de Coagulopatias Congénitas do Hospital de Santa Maria, Lisbon, Portugal.
  • Pinto PR; Life and Health Sciences Research Institute (ICVS), School of Medicine, University of Minho, Braga, Portugal.
  • Salvado R; ICVS / 3B's - PT GovernmentAssociateLaboratory, Braga / Guimarães, Portugal.
  • Dos Santos AA; Centro de Coagulopatias Congénitas do Centro Hospitalar e Universitário de Coimbra (CHUC), Coimbra, Portugal.
  • Silva C; Centro de Referência de Coagulopatias Congénitas do Centro Hospitalar Lisboa Central - Hospital São José, Lisbon, Portugal.
Orphanet J Rare Dis ; 14(1): 211, 2019 09 04.
Article in En | MEDLINE | ID: mdl-31484564

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hemophilia A Type of study: Health_economic_evaluation Aspects: Patient_preference Limits: Adolescent / Child / Child, preschool / Female / Humans / Infant / Male / Newborn Country/Region as subject: Europa Language: En Journal: Orphanet J Rare Dis Journal subject: MEDICINA Year: 2019 Document type: Article Affiliation country: Portugal

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hemophilia A Type of study: Health_economic_evaluation Aspects: Patient_preference Limits: Adolescent / Child / Child, preschool / Female / Humans / Infant / Male / Newborn Country/Region as subject: Europa Language: En Journal: Orphanet J Rare Dis Journal subject: MEDICINA Year: 2019 Document type: Article Affiliation country: Portugal