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Effective and safe treatment of a novel IL2RA deficiency with rapamycin.
Lai, Nannan; Liu, Luyao; Lin, Li; Cui, Chaoqun; Wang, Ying; Min, Qing; Xiong, Ermeng; Wang, Wenjie; Ying, Wenjing; Zhou, Qinhua; Hou, Jia; Sun, Jinqiao; Wang, Ji-Yang; Wang, Xiaochuan.
Affiliation
  • Lai N; Department of Immunology, School of Basic Medical Sciences, Fudan University, Shanghai, China.
  • Liu L; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China.
  • Lin L; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China.
  • Cui C; Department of Immunology, School of Basic Medical Sciences, Fudan University, Shanghai, China.
  • Wang Y; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China.
  • Min Q; Department of Immunology, School of Basic Medical Sciences, Fudan University, Shanghai, China.
  • Xiong E; Department of Immunology, School of Basic Medical Sciences, Fudan University, Shanghai, China.
  • Wang W; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China.
  • Ying W; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China.
  • Zhou Q; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China.
  • Hou J; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China.
  • Sun J; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China. Electronic address: jinqiaosun@fudan.edu.cn.
  • Wang JY; Department of Immunology, School of Basic Medical Sciences, Fudan University, Shanghai, China. Electronic address: wang@fudan.edu.cn.
  • Wang X; Department of Clinical Immunology, Children's Hospital of Fudan University, Shanghai, China. Electronic address: xchwang@shmu.edu.cn.
J Allergy Clin Immunol Pract ; 8(3): 1132-1135.e4, 2020 03.
Article in En | MEDLINE | ID: mdl-31605764

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Sirolimus / Immunologic Deficiency Syndromes Limits: Humans Language: En Journal: J Allergy Clin Immunol Pract Year: 2020 Document type: Article Affiliation country: China Publication country: EEUU / ESTADOS UNIDOS / ESTADOS UNIDOS DA AMERICA / EUA / UNITED STATES / UNITED STATES OF AMERICA / US / USA

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Sirolimus / Immunologic Deficiency Syndromes Limits: Humans Language: En Journal: J Allergy Clin Immunol Pract Year: 2020 Document type: Article Affiliation country: China Publication country: EEUU / ESTADOS UNIDOS / ESTADOS UNIDOS DA AMERICA / EUA / UNITED STATES / UNITED STATES OF AMERICA / US / USA