MicroRNA-Based Therapeutic Perspectives in Myotonic Dystrophy.

López Castel, Arturo; Overby, Sarah Joann; Artero, Rubén

López Castel, Arturo; Overby, Sarah Joann; Artero, Rubén.

Affiliation

López Castel A; Translational Genomics Group, Incliva Health Research Institute, Burjassot, 46100 Valencia, Spain.
Overby SJ; Interdisciplinary Research Structure for Biotechnology and Biomedicine (Eri Biotecmed), University of Valencia, Burjassot, 46100 Valencia, Spain.
Artero R; Translational Genomics Group, Incliva Health Research Institute, Burjassot, 46100 Valencia, Spain.

Int J Mol Sci ; 20(22)2019 Nov 09.

Article in En | MEDLINE | ID: mdl-31717488

Subject(s)

MicroRNAs/genetics; Myotonic Dystrophy/genetics; Alternative Splicing; Animals; CELF1 Protein/genetics; Drug Discovery; Gene Expression Regulation; Genetic Therapy; Humans; Myotonic Dystrophy/therapy; RNA-Binding Proteins/genetics

Key words

CELF1; MBNL proteins; alternative splicing; antisense oligonucleotides; miRNA-based drug; miRNA-targeting drug; microRNA; myotonic dystrophy

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Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: MicroRNAs / Myotonic Dystrophy Limits: Animals / Humans Language: En Journal: Int J Mol Sci Year: 2019 Document type: Article Affiliation country: Spain Country of publication: Switzerland

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