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Fenfluramine for Treatment-Resistant Seizures in Patients With Dravet Syndrome Receiving Stiripentol-Inclusive Regimens: A Randomized Clinical Trial.
Nabbout, Rima; Mistry, Arun; Zuberi, Sameer; Villeneuve, Nathalie; Gil-Nagel, Antonio; Sanchez-Carpintero, Rocio; Stephani, Ulrich; Laux, Linda; Wirrell, Elaine; Knupp, Kelly; Chiron, Catherine; Farfel, Gail; Galer, Bradley S; Morrison, Glenn; Lock, Michael; Agarwal, Anupam; Auvin, Stéphane.
Affiliation
  • Nabbout R; Hôpital Universitaire Necker-Enfants Malades, Service de Neurologie Pédiatrique Centre de Référence Épilepsies Rares, Imagine Institute, Institut National de la Santé et de la Recherche Médicale, Unite Mixté de Recherche 1163, Paris Descartes University, Paris, France.
  • Mistry A; Zogenix, Inc, Emeryville, California.
  • Zuberi S; Paediatric Neurosciences Research Group, Royal Hospital for Children Glasgow, Glasgow, United Kingdom.
  • Villeneuve N; Assistance Publique-Hôpitaux de Marseille, Department of Pediatric Neurology, Hôpital de la Timone, Marseille, France.
  • Gil-Nagel A; Hospital Ruber Internacional, Madrid, Spain.
  • Sanchez-Carpintero R; Pediatric Neurology Unit, Clínica Universidad de Navarra, Pamplona, Spain.
  • Stephani U; Department of Neuropediatrics, Christian-Albrechts-University, Kiel, Germany.
  • Laux L; Ann & Robert H. Lurie Children's Hospital of Chicago, Northwestern University Feinberg School of Medicine, Chicago, Illinois.
  • Wirrell E; Mayo Clinic, Rochester, Minnesota.
  • Knupp K; University of Colorado, Children's Hospital Colorado, Aurora.
  • Chiron C; Pediatric Neurology, Necker-Enfants Malades Hospital, Institut National de la Santé et de la Recherche Médicale Unite 1141, Paris, France.
  • Farfel G; Zogenix, Inc, Emeryville, California.
  • Galer BS; Zogenix, Inc, Emeryville, California.
  • Morrison G; Zogenix, Inc, Emeryville, California.
  • Lock M; Zogenix, Inc, Emeryville, California.
  • Agarwal A; Zogenix, Inc, Emeryville, California.
  • Auvin S; Robert Debré University Hospital, Université de Paris, Institut National de la Santé et de la Recherche Médicale Unite 1141, Paris, France.
JAMA Neurol ; 77(3): 300-308, 2020 03 01.
Article in En | MEDLINE | ID: mdl-31790543

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Epilepsies, Myoclonic / Selective Serotonin Reuptake Inhibitors / Fenfluramine / Drug Resistant Epilepsy Type of study: Clinical_trials / Etiology_studies Limits: Adolescent / Child / Child, preschool / Female / Humans / Male Language: En Journal: JAMA Neurol Year: 2020 Document type: Article Affiliation country: France Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Epilepsies, Myoclonic / Selective Serotonin Reuptake Inhibitors / Fenfluramine / Drug Resistant Epilepsy Type of study: Clinical_trials / Etiology_studies Limits: Adolescent / Child / Child, preschool / Female / Humans / Male Language: En Journal: JAMA Neurol Year: 2020 Document type: Article Affiliation country: France Country of publication: United States