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Clinical trial data available for UX001, aceneuramic acid extended-release.
Bedrosian, Camille L.
Affiliation
  • Bedrosian CL; Ultragenyx Pharmaceutical Inc., Novato, CA, United States. Electronic address: publications@ultragenyx.com.
J Neurol Sci ; 411: 116724, 2020 04 15.
Article in En | MEDLINE | ID: mdl-32058180

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: N-Acetylneuraminic Acid / Distal Myopathies Limits: Humans Language: En Journal: J Neurol Sci Year: 2020 Document type: Article Country of publication: Netherlands

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: N-Acetylneuraminic Acid / Distal Myopathies Limits: Humans Language: En Journal: J Neurol Sci Year: 2020 Document type: Article Country of publication: Netherlands