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Selumetinib in the Treatment of Symptomatic Intractable Plexiform Neurofibromas in Neurofibromatosis Type 1: A Prospective Case Series with Emphasis on Side Effects.
Baldo, Francesco; Grasso, Antonio Giacomo; Cortellazzo Wiel, Luisa; Maestro, Alessandra; Trojniak, Marta Paulina; Murru, Flora Maria; Basso, Luca; Magnolato, Andrea; Bruno, Irene; Barbi, Egidio.
Affiliation
  • Baldo F; Department of Medicine, Surgery and Health Sciences, University of Trieste, Piazzale Europa 1, 34127, Trieste, Italy. francescobaldo11@yahoo.it.
  • Grasso AG; Department of Medicine, Surgery and Health Sciences, University of Trieste, Piazzale Europa 1, 34127, Trieste, Italy.
  • Cortellazzo Wiel L; Department of Medicine, Surgery and Health Sciences, University of Trieste, Piazzale Europa 1, 34127, Trieste, Italy.
  • Maestro A; Pharmacy and Clinical Pharmacology Unit, Institute for Maternal and Child Health, IRCCS Burlo Garofolo, Via dell'Istria 65/1, 34137, Trieste, Italy.
  • Trojniak MP; Pharmacy and Clinical Pharmacology Unit, Institute for Maternal and Child Health, IRCCS Burlo Garofolo, Via dell'Istria 65/1, 34137, Trieste, Italy.
  • Murru FM; Department of Radiology, Institute for Maternal and Child Health, IRCCS Burlo Garofolo, Via dell'Istria 65/1, 34137, Trieste, Italy.
  • Basso L; Department of Radiology, Institute for Maternal and Child Health, IRCCS Giannina Gaslini, Via Gerolamo Gaslini 5, 16147, Genova, Italy.
  • Magnolato A; Department of Pediatrics, Institute for Maternal and Child Health, IRCCS Burlo Garofolo, Via dell'Istria 65/1, 34137, Trieste, Italy.
  • Bruno I; Department of Pediatrics, Institute for Maternal and Child Health, IRCCS Burlo Garofolo, Via dell'Istria 65/1, 34137, Trieste, Italy.
  • Barbi E; Department of Medicine, Surgery and Health Sciences, University of Trieste, Piazzale Europa 1, 34127, Trieste, Italy.
Paediatr Drugs ; 22(4): 417-423, 2020 Aug.
Article in En | MEDLINE | ID: mdl-32533336

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Benzimidazoles / Neurofibromatosis 1 / Neurofibroma, Plexiform Type of study: Diagnostic_studies / Observational_studies Limits: Adolescent / Child / Child, preschool / Female / Humans / Male Language: En Journal: Paediatr Drugs Journal subject: PEDIATRIA / TERAPIA POR MEDICAMENTOS Year: 2020 Document type: Article Affiliation country: Italy

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Benzimidazoles / Neurofibromatosis 1 / Neurofibroma, Plexiform Type of study: Diagnostic_studies / Observational_studies Limits: Adolescent / Child / Child, preschool / Female / Humans / Male Language: En Journal: Paediatr Drugs Journal subject: PEDIATRIA / TERAPIA POR MEDICAMENTOS Year: 2020 Document type: Article Affiliation country: Italy