Nonsense Suppression Therapy: New Hypothesis for the Treatment of Inherited Bone Marrow Failure Syndromes.
Int J Mol Sci
; 21(13)2020 Jun 30.
Article
in En
| MEDLINE
| ID: mdl-32630050
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Oxadiazoles
/
Codon, Nonsense
/
Nonsense Mediated mRNA Decay
/
Congenital Bone Marrow Failure Syndromes
/
Aminoglycosides
Limits:
Humans
Language:
En
Journal:
Int J Mol Sci
Year:
2020
Document type:
Article
Affiliation country:
Italy
Country of publication:
Switzerland