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Nonsense Suppression Therapy: New Hypothesis for the Treatment of Inherited Bone Marrow Failure Syndromes.
Bezzerri, Valentino; Api, Martina; Allegri, Marisole; Fabrizzi, Benedetta; Corey, Seth J; Cipolli, Marco.
Affiliation
  • Bezzerri V; Cystic Fibrosis Center, Azienda Ospedaliero Universitaria Ospedali Riuniti, Via Conca 71, 60126 Ancona, Italy.
  • Api M; Cystic Fibrosis Center, Azienda Ospedaliero Universitaria Ospedali Riuniti, Via Conca 71, 60126 Ancona, Italy.
  • Allegri M; Cystic Fibrosis Center, Azienda Ospedaliero Universitaria Ospedali Riuniti, Via Conca 71, 60126 Ancona, Italy.
  • Fabrizzi B; Cystic Fibrosis Center, Azienda Ospedaliero Universitaria Ospedali Riuniti, Via Conca 71, 60126 Ancona, Italy.
  • Corey SJ; Department of Pediatric Hematology/Oncology and Stem Cell Transplantation, Cleveland Clinic, Cleveland, OH 44195, USA.
  • Cipolli M; Cystic Fibrosis Center, Azienda Ospedaliera Universitaria Integrata, P.le A. Stefani 1, 37126 Verona, Italy.
Int J Mol Sci ; 21(13)2020 Jun 30.
Article in En | MEDLINE | ID: mdl-32630050

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oxadiazoles / Codon, Nonsense / Nonsense Mediated mRNA Decay / Congenital Bone Marrow Failure Syndromes / Aminoglycosides Limits: Humans Language: En Journal: Int J Mol Sci Year: 2020 Document type: Article Affiliation country: Italy Country of publication: Switzerland

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oxadiazoles / Codon, Nonsense / Nonsense Mediated mRNA Decay / Congenital Bone Marrow Failure Syndromes / Aminoglycosides Limits: Humans Language: En Journal: Int J Mol Sci Year: 2020 Document type: Article Affiliation country: Italy Country of publication: Switzerland