Your browser doesn't support javascript.
loading
Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy.
Sergott, Robert C; Amorelli, Giulia M; Baranello, Giovanni; Barreau, Emmanuel; Beres, Shannon; Kane, Steven; Mercuri, Eugenio; Orazi, Lorenzo; SantaMaria, Melissa; Tremolada, Gemma; Santarsiero, Diletta; Waskowska, Agnieszka; Yashiro, Shigeko; Denk, Nora; Fürst-Recktenwald, Sabine; Gerber, Marianne; Gorni, Ksenija; Jaber, Birgit; Jacobsen, Bjoern; Mueller, Lutz; Nave, Stephane; Scalco, Renata S; Marzoli, Stefania B.
Affiliation
  • Sergott RC; Department of Neuro-Ophthalmology, Wills Eye Hospital, Philadelphia, USA.
  • Amorelli GM; Annesley EyeBrain Center, Thomas Jefferson University, Philadelphia, USA.
  • Baranello G; Paediatric Neurology and Nemo Center, Catholic University and Policlinico Gemelli, Rome, Italy.
  • Barreau E; The Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health University College London, & Great Ormond Street Hospital Trust, London, UK.
  • Beres S; Developmental Neurology Unit, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.
  • Kane S; Institute of Myology, Paris, France.
  • Mercuri E; Department of Neurology, Department of Ophthalmology, Stanford University, Palo Alto, California, USA.
  • Orazi L; Columbia University Medical Center, New York, USA.
  • SantaMaria M; Paediatric Neurology and Nemo Center, Catholic University and Policlinico Gemelli, Rome, Italy.
  • Tremolada G; Paediatric Neurology and Nemo Center, Catholic University and Policlinico Gemelli, Rome, Italy.
  • Santarsiero D; Annesley EyeBrain Center, Thomas Jefferson University, Philadelphia, USA.
  • Waskowska A; Neuro-Ophthalmology Center, Ophthalmology Department, IRCCS Istituto Auxologico Italiano, Milan, Italy.
  • Yashiro S; Neuro-Ophthalmology Center, Ophthalmology Department, IRCCS Istituto Auxologico Italiano, Milan, Italy.
  • Denk N; Department of Developmental Neurology, Medical University of Gdansk, Gdansk, Poland.
  • Fürst-Recktenwald S; Department of Ophthalmology, National Center for Global Health and Medicine (NCGM), Tokyo, Japan.
  • Gerber M; Roche Pharma Research and Early Development, Pharmaceutical Sciences, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
  • Gorni K; Pharma Development Neurology, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
  • Jaber B; Pharma Development, Safety, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
  • Jacobsen B; PDMA Neuroscience and Rare Disease, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
  • Mueller L; Pharma Development, Safety, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
  • Nave S; Roche Pharma Research and Early Development, Pharmaceutical Sciences, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
  • Scalco RS; Roche Pharma Research and Early Development, Pharmaceutical Sciences, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
  • Marzoli SB; Roche Pharma Research and Early Development, Pharmaceutical Sciences, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd, Basel, Switzerland.
Ann Clin Transl Neurol ; 8(1): 54-65, 2021 01.
Article in En | MEDLINE | ID: mdl-33231373
Subject(s)
Fulltext
Add to My VHL
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Pyrimidines / Retina / Azo Compounds / Muscular Atrophy, Spinal / Neuromuscular Agents Limits: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male / Middle aged Language: En Journal: Ann Clin Transl Neurol Year: 2021 Document type: Article Affiliation country: United States Country of publication: United States
Fulltext
Add to My VHL
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Pyrimidines / Retina / Azo Compounds / Muscular Atrophy, Spinal / Neuromuscular Agents Limits: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male / Middle aged Language: En Journal: Ann Clin Transl Neurol Year: 2021 Document type: Article Affiliation country: United States Country of publication: United States