Preclinical Systemic Delivery of Adeno-Associated α-Sarcoglycan Gene Transfer for Limb-Girdle Muscular Dystrophy.
Hum Gene Ther
; 32(7-8): 390-404, 2021 04.
Article
in En
| MEDLINE
| ID: mdl-33349138
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Muscular Dystrophies, Limb-Girdle
/
Sarcoglycanopathies
Type of study:
Prognostic_studies
/
Risk_factors_studies
Limits:
Animals
/
Humans
Language:
En
Journal:
Hum Gene Ther
Journal subject:
GENETICA MEDICA
/
TERAPEUTICA
Year:
2021
Document type:
Article
Affiliation country:
United States
Country of publication:
United States