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Efficient correction of Duchenne muscular dystrophy mutations by SpCas9 and dual gRNAs.
Xiang, Xi; Zhao, Xiaoying; Pan, Xiaoguang; Dong, Zhanying; Yu, Jiaying; Li, Siyuan; Liang, Xue; Han, Peng; Qu, Kunli; Jensen, Jonas Brorson; Farup, Jean; Wang, Fei; Petersen, Trine Skov; Bolund, Lars; Teng, Huajing; Lin, Lin; Luo, Yonglun.
Affiliation
  • Xiang X; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Zhao X; Department of Biomedicine, Aarhus University, Aarhus 8000, Denmark.
  • Pan X; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Dong Z; Department of Biomedicine, Aarhus University, Aarhus 8000, Denmark.
  • Yu J; BGI Education Center, University of Chinese Academy of Sciences, Shenzhen 518083, China.
  • Li S; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Liang X; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Han P; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Qu K; BGI Education Center, University of Chinese Academy of Sciences, Shenzhen 518083, China.
  • Jensen JB; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Farup J; BGI Education Center, University of Chinese Academy of Sciences, Shenzhen 518083, China.
  • Wang F; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Petersen TS; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Bolund L; Lars Bolund Institute of Regenerative Medicine, Qingdao-Europe Advanced Institute for Life Sciences, BGI-Qingdao, BGI-Shenzhen, Qingdao 266555, China.
  • Teng H; Department of Biomedicine, Aarhus University, Aarhus 8000, Denmark.
  • Lin L; Steno Diabetes Center Aarhus, Aarhus University Hospital, Aarhus 8200, Denmark.
  • Luo Y; Department of Biomedicine, Aarhus University, Aarhus 8000, Denmark.
Mol Ther Nucleic Acids ; 24: 403-415, 2021 Jun 04.
Article in En | MEDLINE | ID: mdl-33868784

Full text: 1 Collection: 01-internacional Database: MEDLINE Type of study: Prognostic_studies Language: En Journal: Mol Ther Nucleic Acids Year: 2021 Document type: Article Affiliation country: China Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Type of study: Prognostic_studies Language: En Journal: Mol Ther Nucleic Acids Year: 2021 Document type: Article Affiliation country: China Country of publication: United States