The GM2 gangliosidoses: Unlocking the mysteries of pathogenesis and treatment.
Neurosci Lett
; 764: 136195, 2021 11 01.
Article
in En
| MEDLINE
| ID: mdl-34450229
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Genetic Therapy
/
Gangliosidoses, GM2
/
Beta-Hexosaminidase alpha Chain
/
Beta-Hexosaminidase beta Chain
/
Enzyme Replacement Therapy
Type of study:
Etiology_studies
Limits:
Animals
/
Humans
Language:
En
Journal:
Neurosci Lett
Year:
2021
Document type:
Article
Affiliation country:
United States
Country of publication:
Ireland