Treatment of GM2 Gangliosidosis in Adult Sandhoff Mice Using an Intravenous Self-Complementary Hexosaminidase Vector.
Curr Gene Ther
; 22(3): 262-276, 2022.
Article
in En
| MEDLINE
| ID: mdl-34530708
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Sandhoff Disease
/
Gangliosidoses, GM2
Limits:
Animals
/
Humans
Language:
En
Journal:
Curr Gene Ther
Journal subject:
GENETICA MEDICA
/
TERAPEUTICA
Year:
2022
Document type:
Article
Affiliation country:
Canada
Country of publication:
United Arab Emirates