Antisense oligonucleotide splicing modulation as a novel Cystic Fibrosis therapeutic approach for the W1282X nonsense mutation.
J Cyst Fibros
; 21(4): 630-636, 2022 07.
Article
in En
| MEDLINE
| ID: mdl-34972649
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Cystic Fibrosis Transmembrane Conductance Regulator
/
Cystic Fibrosis
Limits:
Humans
Language:
En
Journal:
J Cyst Fibros
Year:
2022
Document type:
Article
Affiliation country:
Israel
Country of publication:
Netherlands