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Eptacog beta efficacy and safety in the treatment and control of bleeding in paediatric subjects (<12 years) with haemophilia A or B with inhibitors.
Pipe, Steven W; Hermans, Cédric; Chitlur, Meera; Carcao, Manuel; Castaman, Giancarlo; Davis, Joanna A; Ducore, Jonathan; Dunn, Amy L; Escobar, Miguel; Journeycake, Janna; Khan, Osman; Mahlangu, Johnny; Meeks, Shannon L; Mitha, Ismail Haroon; Négrier, Claude; Nowak-Göttl, Ulrike; Recht, Michael; Chrisentery-Singleton, Tammuella; Stasyshyn, Oleksandra; Vilchevska, Kateryna V; Martinez, Laura Villarreal; Wang, Michael; Windyga, Jerzy; Young, Guy; Alexander, W Allan; Bonzo, Daniel; Macie, Christopher; Mitchell, Ian S; Sauty, Evelyne; Wilkinson, Thomas A; Shapiro, Amy D.
Affiliation
  • Pipe SW; University of Michigan, Ann Arbor, Michigan, USA.
  • Hermans C; Cliniques Saint-Luc, Université Catholique de Louvain, Brussels, Belgium.
  • Chitlur M; Children's Hospital of Michigan, Central Michigan University, Detroit, Michigan, USA.
  • Carcao M; The Hospital for Sick Children, Toronto, Ontario, Canada.
  • Castaman G; Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy.
  • Davis JA; Pediatric Hemophilia Treatment Center, University of Miami, Miami, Florida, USA.
  • Ducore J; Hematology/Oncology Clinic, University of California at Davis, Sacramento, California, USA.
  • Dunn AL; Nationwide Children's Hospital, Department of Pediatrics at The Ohio State University College of Medicine, Columbus, Ohio, USA.
  • Escobar M; University of Texas Health Science Center at Houston, Houston, Texas, USA.
  • Journeycake J; Oklahoma Center for Bleeding and Clotting Disorders at OU Health, Oklahoma City, Oklahoma, USA.
  • Khan O; Oklahoma Center for Bleeding and Clotting Disorders at OU Health, Oklahoma City, Oklahoma, USA.
  • Mahlangu J; Hemophilia Comprehensive Care Center, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa.
  • Meeks SL; Emory University and Aflac Cancer and Blood Disorders Center of Children's Healthcare of Atlanta, Atlanta, Georgia, USA.
  • Mitha IH; Lakeview Hospital, Benoni, Gauteng, South Africa.
  • Négrier C; Edouard Herriot University Hospital, Lyon, France.
  • Nowak-Göttl U; Institute of Clinical Chemistry, University Hospital Schleswig-Holstein, Kiel, Germany.
  • Recht M; American Thrombosis and Hemostasis Network, Rochester, New York, USA.
  • Chrisentery-Singleton T; Oregon Health & Science University, Portland, Oregon, USA.
  • Stasyshyn O; Louisiana Center for Advanced Medicine, Slidell, Louisiana, USA.
  • Vilchevska KV; Institute of Blood Pathology and Transfusion Medicine, Lviv, Ukraine.
  • Martinez LV; National Specialized Children's Hospital Okhmatdyt, Kyiv, Ukraine.
  • Wang M; Dr. José Eleuterio González Monterrey University Hospital, Monterrey, Nuevo León, México.
  • Windyga J; Hemophilia and Thrombosis Center, University of Colorado, Aurora, Colorado, USA.
  • Young G; Department of Hemostasis Disorders and Internal Medicine, Institute of Hematology and Transfusion Medicine, Warsaw, Poland.
  • Alexander WA; Children's Hospital Los Angeles, Los Angeles, California, USA.
  • Bonzo D; Keck School of Medicine, University of Southern California, Los Angeles, California, USA.
  • Macie C; Aoede Associates, Athens, Texas, USA.
  • Mitchell IS; LFB-USA, Inc., Framingham, Massachusetts, USA.
  • Sauty E; HEMA Biologics, LLC, Louisville, Kentucky, USA.
  • Wilkinson TA; HEMA Biologics, LLC, Louisville, Kentucky, USA.
  • Shapiro AD; LFB, Laboratoire français du fractionnement et des biotechnologies, Les Ulis, France.
Haemophilia ; 28(4): 548-556, 2022 Jul.
Article in En | MEDLINE | ID: mdl-35475308

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Recombinant Proteins / Factor VIIa / Hemophilia A Type of study: Clinical_trials / Etiology_studies Limits: Child / Humans Language: En Journal: Haemophilia Journal subject: HEMATOLOGIA Year: 2022 Document type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Recombinant Proteins / Factor VIIa / Hemophilia A Type of study: Clinical_trials / Etiology_studies Limits: Child / Humans Language: En Journal: Haemophilia Journal subject: HEMATOLOGIA Year: 2022 Document type: Article Affiliation country: United States