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Bone Remodeling in an Mps-1h Girl after Hematopoietic Stem Cell Transplantation along with Enzymatic Replacement Therapy.
Tummolo, Albina; Brunetti, Giacomina; Piacente, Laura; Marzollo, Antonio; Biffi, Alessandra; Burlina, Alberto; Faienza, Maria Felicia.
Affiliation
  • Tummolo A; Department of Metabolic Diseases, Clinical Genetics and Diabetology, Giovanni XXIII Children Hospital, Azienda Ospedaliero-Universitaria Consorziale, Bari, Italy.
  • Brunetti G; Department of Biosciences, Biotechnologies and Biopharmaceutics, University of Bari, Bari, Italy.
  • Piacente L; Department of Biomedical Sciences and Human Oncology, Pediatric Unit, University of Bari "A. Moro", Italy.
  • Marzollo A; Pediatric Hematology, Oncology and Stem Cell Transplant Division, Padua University Hospital, Padua, Italy.
  • Biffi A; Fondazione Città della Speranza, Istituto di Ricerca Pediatrica, Padua, Italy.
  • Burlina A; Pediatric Hematology, Oncology and Stem Cell Transplant Division, Padua University Hospital, Padua, Italy.
  • Faienza MF; Maternal and Child Health Department, Padua University, Padua, Italy.
Article in En | MEDLINE | ID: mdl-35619307

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Lysosomal Storage Diseases / Mucopolysaccharidosis I / Hematopoietic Stem Cell Transplantation Limits: Child / Female / Humans Language: En Journal: Endocr Metab Immune Disord Drug Targets Journal subject: ALERGIA E IMUNOLOGIA / ENDOCRINOLOGIA / METABOLISMO / TERAPIA POR MEDICAMENTOS Year: 2022 Document type: Article Affiliation country: Italy Country of publication: United Arab Emirates

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Lysosomal Storage Diseases / Mucopolysaccharidosis I / Hematopoietic Stem Cell Transplantation Limits: Child / Female / Humans Language: En Journal: Endocr Metab Immune Disord Drug Targets Journal subject: ALERGIA E IMUNOLOGIA / ENDOCRINOLOGIA / METABOLISMO / TERAPIA POR MEDICAMENTOS Year: 2022 Document type: Article Affiliation country: Italy Country of publication: United Arab Emirates