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Parents' Experience of Administering Vosoritide: A Daily Injectable for Children with Achondroplasia.
NiMhurchadha, Sinead; Butler, Karen; Argent, Rob; Palm, Katja; Baujat, Genevieve; Cormier-Daire, Valerie; Mohnike, Klaus.
Affiliation
  • NiMhurchadha S; S3 Connected Health, Dublin, Ireland. Sinead.NiMhurchadha@S3Connectedhealth.com.
  • Butler K; S3 Connected Health, Dublin, Ireland.
  • Argent R; School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons (RCSI), University of Medicine and Health Sciences, Dublin, Ireland.
  • Palm K; Universitätskinderklinik Magdeburg, Otto von Guericke University, Magdeburg, Germany.
  • Baujat G; Reference Center for Skeletal Dysplasia, Hopital Necker-Enfants Malades Hopital Necker Enfants Malades, Paris University, Paris, France.
  • Cormier-Daire V; Reference Center for Skeletal Dysplasia, Hopital Necker-Enfants Malades Hopital Necker Enfants Malades, Paris University, Paris, France.
  • Mohnike K; INSERM UMR 1163, Imagine Institute, Paris Cité University, Paris, France.
Adv Ther ; 40(5): 2457-2470, 2023 05.
Article in En | MEDLINE | ID: mdl-37017912

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Quality of Life / Achondroplasia Type of study: Qualitative_research Aspects: Patient_preference Limits: Child / Humans / Newborn Language: En Journal: Adv Ther Journal subject: TERAPEUTICA Year: 2023 Document type: Article Affiliation country: Ireland Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Quality of Life / Achondroplasia Type of study: Qualitative_research Aspects: Patient_preference Limits: Child / Humans / Newborn Language: En Journal: Adv Ther Journal subject: TERAPEUTICA Year: 2023 Document type: Article Affiliation country: Ireland Country of publication: United States