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Gene transfer therapy in children with spinal muscular atrophy: A single-center experience with a cohort of 25 children.
Chencheri, Nidheesh; Alexander, Gail; Nugud, Ahmed; Majadas, Eurose; Salim, Haneen; Prudhomme, Katy; DeJager, Noleen; Janardhanan, Vaishnavi Shetty; Elbashir, Haitham.
Affiliation
  • Chencheri N; Neurosciences Center of Excellence, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • Alexander G; Neurosciences Center of Excellence, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • Nugud A; Neurosciences Center of Excellence, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • Majadas E; Rehabilitation Department, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • Salim H; Rehabilitation Department, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • Prudhomme K; Rehabilitation Department, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • DeJager N; Rehabilitation Department, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • Janardhanan VS; Rehabilitation Department, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
  • Elbashir H; Neurosciences Center of Excellence, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
Muscle Nerve ; 68(3): 269-277, 2023 09.
Article in En | MEDLINE | ID: mdl-37392188

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood Type of study: Risk_factors_studies Limits: Child / Humans / Infant Country/Region as subject: Europa Language: En Journal: Muscle Nerve Year: 2023 Document type: Article Affiliation country: United Arab Emirates Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood Type of study: Risk_factors_studies Limits: Child / Humans / Infant Country/Region as subject: Europa Language: En Journal: Muscle Nerve Year: 2023 Document type: Article Affiliation country: United Arab Emirates Country of publication: United States