Gene transfer therapy in children with spinal muscular atrophy: A single-center experience with a cohort of 25 children.
Muscle Nerve
; 68(3): 269-277, 2023 09.
Article
in En
| MEDLINE
| ID: mdl-37392188
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Muscular Atrophy, Spinal
/
Spinal Muscular Atrophies of Childhood
Type of study:
Risk_factors_studies
Limits:
Child
/
Humans
/
Infant
Country/Region as subject:
Europa
Language:
En
Journal:
Muscle Nerve
Year:
2023
Document type:
Article
Affiliation country:
United Arab Emirates
Country of publication:
United States