Your browser doesn't support javascript.
loading
Gene therapy for glycogen storage diseases.
Koeberl, Dwight D; Koch, Rebecca L; Lim, Jeong-A; Brooks, Elizabeth D; Arnson, Benjamin D; Sun, Baodong; Kishnani, Priya S.
Affiliation
  • Koeberl DD; Division of Medical Genetics, Department of Pediatrics, Duke University Medical School, Durham, North Carolina, USA.
  • Koch RL; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, North Carolina, USA.
  • Lim JA; Division of Medical Genetics, Department of Pediatrics, Duke University Medical School, Durham, North Carolina, USA.
  • Brooks ED; Division of Medical Genetics, Department of Pediatrics, Duke University Medical School, Durham, North Carolina, USA.
  • Arnson BD; Division of Medical Genetics, Department of Pediatrics, Duke University Medical School, Durham, North Carolina, USA.
  • Sun B; Department of Molecular Genetics and Microbiology, Duke University Medical Center, Durham, North Carolina, USA.
  • Kishnani PS; Division of Medical Genetics, Department of Pediatrics, Duke University Medical School, Durham, North Carolina, USA.
J Inherit Metab Dis ; 47(1): 93-118, 2024 Jan.
Article in En | MEDLINE | ID: mdl-37421310

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease / Glycogen Storage Disease Type I / Glycogen Storage Disease Type II / Carcinoma, Hepatocellular / Liver Neoplasms Type of study: Prognostic_studies Limits: Animals Language: En Journal: J Inherit Metab Dis Year: 2024 Document type: Article Affiliation country: United States Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease / Glycogen Storage Disease Type I / Glycogen Storage Disease Type II / Carcinoma, Hepatocellular / Liver Neoplasms Type of study: Prognostic_studies Limits: Animals Language: En Journal: J Inherit Metab Dis Year: 2024 Document type: Article Affiliation country: United States Country of publication: United States