One transgene, two myopathies: an MTM1 'cross gene therapy' for BIN1 deficiency?

Asgarian, Zeinab; Siam, Ala'a; Counsell, John R

Asgarian, Zeinab; Siam, Ala'a; Counsell, John R.

Affiliation

Asgarian Z; Research Department of Targeted Intervention, UCL Division of Surgery and Interventional Science, Charles Bell House, London, UK.
Siam A; Research Department of Targeted Intervention, UCL Division of Surgery and Interventional Science, Charles Bell House, London, UK.
Counsell JR; Research Department of Targeted Intervention, UCL Division of Surgery and Interventional Science, Charles Bell House, London, UK.

Brain ; 146(10): 3966-3968, 2023 10 03.

Article in En | MEDLINE | ID: mdl-37738144

Subject(s)

Myopathies, Structural, Congenital; Humans; Myopathies, Structural, Congenital/genetics; Myopathies, Structural, Congenital/therapy; Nuclear Proteins/genetics; Tumor Suppressor Proteins/genetics; Adaptor Proteins, Signal Transducing/genetics

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Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Myopathies, Structural, Congenital Limits: Humans Language: En Journal: Brain Year: 2023 Document type: Article Affiliation country: United kingdom

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