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Landmark endorsement of a global registry: The European Medicines Agency (EMA) Committee for Medicinal Products for Human Use (CHMP), publicly endorses World Federation of Hemophilia Gene Therapy Registry as global standard.
Konkle, Barbara A; Peyvandi, Flora; Coffin, Donna; Naccache, Mayss; Youttananukorn, Toong; Pierce, Glenn F.
Affiliation
  • Konkle BA; Washington Center for Bleeding Disorders, University of Washington, Seattle, Washington, USA.
  • Peyvandi F; International Society on Thrombosis and Hemostasis, Carrboro, North Carolina, USA.
  • Coffin D; World Federation of Hemophilia, Montreal, Quebec, Canada.
  • Naccache M; World Federation of Hemophilia, Montreal, Quebec, Canada.
  • Youttananukorn T; World Federation of Hemophilia, Montreal, Quebec, Canada.
  • Pierce GF; World Federation of Hemophilia, Montreal, Quebec, Canada.
Haemophilia ; 30(1): 232-235, 2024 Jan.
Article in En | MEDLINE | ID: mdl-38111095

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hemophilia A Limits: Humans Country/Region as subject: Europa Language: En Journal: Haemophilia Journal subject: HEMATOLOGIA Year: 2024 Document type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hemophilia A Limits: Humans Country/Region as subject: Europa Language: En Journal: Haemophilia Journal subject: HEMATOLOGIA Year: 2024 Document type: Article Affiliation country: United States
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