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Neurocognitive assessment platform for clinical trials in PKU: White paper developed by the NPKUA neurocognitive workgroup.
Waisbren, Susan E; Christ, Shawn E; Bilder, Deborah A; Bjoraker, Kendra J; Bolton, Scout; Chamberlin, Sarah; Grant, Mitzie L; Janzen, Darren M; Katz, Rachel; Lubliner, Eugene; Martin, Arianna; McQueen, Kelsey; Moshkovich, Olga; Nguyen-Driver, Mina; Shim, Soo; Stefanatos, Arianna K; Wilkening, Greta; Harding, Cary.
Affiliation
  • Waisbren SE; Boston Children's Hospital and Harvard Medical School, Boston, MA, United States of America. Electronic address: Susan.waisbren@childrens.harvard.edu.
  • Christ SE; Clinical Neuropsychology Laboratory, University of Missouri, Columbia, MO, United States of America.
  • Bilder DA; Huntsman Mental Health Institute, University of Utah, Salt Lake City, UT, United States of America.
  • Bjoraker KJ; 3:1 Neuropsychology Consultants, PLLC, Aurora, CO, United States of America.
  • Bolton S; Clinical Neuropsychology Laboratory, University of Missouri, Columbia, MO, United States of America.
  • Chamberlin S; flok Health.org (advocacy and research organization), Montclair, NJ, United States of America.
  • Grant ML; Tower Health Medical Group, St. Christopher's Hospital for Children, and Drexel College of Medicine, Philadelphia, PA, United States of America.
  • Janzen DM; Doernbecher Children's Hospital and Oregon Health & Science University, Portland, OR, United States of America.
  • Katz R; Ann & Robert H. Lurie Children's Hospital, Division of Genetics, Genomics and Metabolism, Chicago, IL, United States of America.
  • Lubliner E; Lubliner Psychological Services, Miller Place, NY and Hofstra University, Hempstead, NY, United States of America.
  • Martin A; Department of Pediatrics, Section of Neurology, Children's Hospital Colorado and University of Colorado School of Medicine, Aurora, CO, United States of America.
  • McQueen K; National PKU Alliance, United States of America.
  • Moshkovich O; ICON Insights, Evidence and Value, Raleigh, NC, United States of America.
  • Nguyen-Driver M; University of Arkansas for Medical Sciences, Little Rock, AR, United States of America.
  • Shim S; Ann & Robert H. Lurie Children's Hospital, Division of Genetics, Genomics and Metabolism, Chicago, IL, United States of America.
  • Stefanatos AK; Children's Hospital of Philadelphia, Philadelphia, PA, United States of America.
  • Wilkening G; Children's Hospital of Colorado, University of Colorado Schools of Medicine and Public Health, Aurora, CO, United States of America.
  • Harding C; Doernbecher Children's Hospital and Oregon Health & Science University, Portland, OR, United States of America.
Mol Genet Metab ; 143(1-2): 108555, 2024 Jul 25.
Article in En | MEDLINE | ID: mdl-39089209

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Mol Genet Metab Journal subject: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Year: 2024 Document type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Mol Genet Metab Journal subject: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Year: 2024 Document type: Article