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Sustained correction of motoneuron histopathology following intramuscular delivery of AAV in pompe mice.
Elmallah, Mai K; Falk, Darin J; Nayak, Sushrusha; Federico, Roland A; Sandhu, Milapjit S; Poirier, Amy; Byrne, Barry J; Fuller, David D.
Afiliación
  • Elmallah MK; Department of Pediatrics, Division of Pulmonary Medicine, College of Medicine, University of Florida, Gainesville, Florida, USA.
  • Falk DJ; 1] Department of Pediatrics, Divisions of Cellular and Molecular Therapy and Pediatric Cardiology, College of Medicine, University of Florida, Gainesville, Florida, USA [2] Powell Gene Therapy Center, University of Florida, Gainesville, Florida, USA.
  • Nayak S; 1] Department of Pediatrics, Divisions of Cellular and Molecular Therapy and Pediatric Cardiology, College of Medicine, University of Florida, Gainesville, Florida, USA [2] Powell Gene Therapy Center, University of Florida, Gainesville, Florida, USA.
  • Federico RA; Department of Physical Therapy, College of Public Health and Health Professions, University of Florida, Gainesville, Florida, USA.
  • Sandhu MS; Department of Physical Therapy, College of Public Health and Health Professions, University of Florida, Gainesville, Florida, USA.
  • Poirier A; Department of Neuroscience, College of Medicine, University of Florida, Gainesville, Florida, USA.
  • Byrne BJ; 1] Department of Pediatrics, Divisions of Cellular and Molecular Therapy and Pediatric Cardiology, College of Medicine, University of Florida, Gainesville, Florida, USA [2] Powell Gene Therapy Center, University of Florida, Gainesville, Florida, USA.
  • Fuller DD; 1] Department of Physical Therapy, College of Public Health and Health Professions, University of Florida, Gainesville, Florida, USA [2] McKnight Brain Institute, University of Florida, Gainesville, Florida, USA.
Mol Ther ; 22(4): 702-12, 2014 Apr.
Article en En | MEDLINE | ID: mdl-24336173

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Enfermedad del Almacenamiento de Glucógeno Tipo II / Alfa-Glucosidasas / Neuronas Motoras Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2014 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Enfermedad del Almacenamiento de Glucógeno Tipo II / Alfa-Glucosidasas / Neuronas Motoras Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2014 Tipo del documento: Article País de afiliación: Estados Unidos