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A randomized, placebo-controlled, double-blind study of sapropterin to treat ADHD symptoms and executive function impairment in children and adults with sapropterin-responsive phenylketonuria.
Burton, B; Grant, M; Feigenbaum, A; Singh, R; Hendren, R; Siriwardena, K; Phillips, J; Sanchez-Valle, A; Waisbren, S; Gillis, J; Prasad, S; Merilainen, M; Lang, W; Zhang, C; Yu, S; Stahl, S.
Afiliación
  • Burton B; The Ann and Robert H. Lurie Children's Hospital and the Northwestern University Feinberg School of Medicine, Chicago, IL, USA. Electronic address: BBurton@luriechildrens.org.
  • Grant M; Drexel University College of Medicine, Philadelphia, PA, USA.
  • Feigenbaum A; The Hospital for Sick Children and University of Toronto, ON, Canada.
  • Singh R; Emory University School of Medicine, Decatur, GA, USA.
  • Hendren R; University of California, San Francisco, San Francisco, CA, USA.
  • Siriwardena K; Drexel University College of Medicine, Philadelphia, PA, USA.
  • Phillips J; Vanderbilt University School of Medicine, Nashville, TN, USA.
  • Sanchez-Valle A; University of South Florida and Tampa General Hospital, Tampa, FL, USA.
  • Waisbren S; Boston Children's Hospital, Boston, MA, USA.
  • Gillis J; IWK Health Centre Maritime Medical Genetics Services, Halifax, NS, Canada.
  • Prasad S; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Merilainen M; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Lang W; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Zhang C; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Yu S; BioMarin Pharmaceutical Inc., Novato, CA, USA.
  • Stahl S; University of California, San Diego School of Medicine, San Diego, CA, USA.
Mol Genet Metab ; 114(3): 415-24, 2015 Mar.
Article en En | MEDLINE | ID: mdl-25533024

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Fenilalanina / Fenilcetonurias / Trastorno por Déficit de Atención con Hiperactividad / Biopterinas / Función Ejecutiva Tipo de estudio: Clinical_trials / Diagnostic_studies Límite: Adolescent / Adult / Child / Female / Humans / Male Idioma: En Revista: Mol Genet Metab Asunto de la revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Año: 2015 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Fenilalanina / Fenilcetonurias / Trastorno por Déficit de Atención con Hiperactividad / Biopterinas / Función Ejecutiva Tipo de estudio: Clinical_trials / Diagnostic_studies Límite: Adolescent / Adult / Child / Female / Humans / Male Idioma: En Revista: Mol Genet Metab Asunto de la revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Año: 2015 Tipo del documento: Article