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Gene therapy in monogenic congenital myopathies.
Guan, Xuan; Goddard, Melissa A; Mack, David L; Childers, Martin K.
Afiliación
  • Guan X; Department of Physiology and Pharmacology, School of Medicine, Wake Forest University Health Sciences, Winston-Salem, NC, USA; Department of Rehabilitation Medicine, University of Washington, Seattle, WA, USA; Institute for Stem Cell and Regenerative Medicine, University of Washington, Seattle, WA,
  • Goddard MA; Department of Physiology and Pharmacology, School of Medicine, Wake Forest University Health Sciences, Winston-Salem, NC, USA; Department of Rehabilitation Medicine, University of Washington, Seattle, WA, USA; Institute for Stem Cell and Regenerative Medicine, University of Washington, Seattle, WA,
  • Mack DL; Department of Rehabilitation Medicine, University of Washington, Seattle, WA, USA; Institute for Stem Cell and Regenerative Medicine, University of Washington, Seattle, WA, USA.
  • Childers MK; Department of Rehabilitation Medicine, University of Washington, Seattle, WA, USA; Institute for Stem Cell and Regenerative Medicine, University of Washington, Seattle, WA, USA. Electronic address: mkc8@uw.edu.
Methods ; 99: 91-8, 2016 Apr 15.
Article en En | MEDLINE | ID: mdl-26454198

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Miopatías Estructurales Congénitas Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Methods Asunto de la revista: BIOQUIMICA Año: 2016 Tipo del documento: Article Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Miopatías Estructurales Congénitas Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Methods Asunto de la revista: BIOQUIMICA Año: 2016 Tipo del documento: Article Pais de publicación: Estados Unidos