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Patient's weight can decide about spending millions on enzyme replacement therapy in MPS II.
Bik-Multanowski, Miroslaw; Jamroz, Ewa; Kaluzny, Lukasz; Pronicka, Ewa; Rokicki, Dariusz; Starostecka, Ewa; Sykut-Cegielska, Jolanta; Walczak, Mieczyslaw.
Afiliación
  • Bik-Multanowski M; Department of Medical Genetics, Jagiellonian University, Medical College, Krakow, Poland.
  • Jamroz E; School of Medicine in Katowice, Department of Paediatrics and Developmental Age Neurology, Medical University of Silesia, Katowice, Poland.
  • Kaluzny L; Department of Pediatric Gastroenterology and Metabolism, Medical University, Poznan, Poland.
  • Pronicka E; Department of Pediatrics, Nutrition and Metabolic Diseases, The Children's Memorial Health Institute, Warszawa, Poland.
  • Rokicki D; Department of Pediatrics, Nutrition and Metabolic Diseases, The Children's Memorial Health Institute, Warszawa, Poland.
  • Starostecka E; Metabolic Department, Polish Mother's Health Memorial Institute, Lodz, Poland.
  • Sykut-Cegielska J; Screening Department, Institute of Mother and Child, Warszawa, Poland.
  • Walczak M; Department of Paediatric Endocrinology and Diabetology, Pomeranian Medical University in Szczecin, Poland.
Mol Genet Metab Rep ; 6: 5-7, 2016 Mar.
Article en En | MEDLINE | ID: mdl-27014570

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Mol Genet Metab Rep Año: 2016 Tipo del documento: Article País de afiliación: Polonia Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Mol Genet Metab Rep Año: 2016 Tipo del documento: Article País de afiliación: Polonia Pais de publicación: Estados Unidos