A Phase 4 Prospective Study in Patients with Adult Pompe Disease Treated with Alglucosidase Alfa.

Thurberg, Beth L; Carlier, Pierre; Kissel, John T; Schoser, Benedikt; Pestronk, Alan; Barohn, Richard J; Goker-Alpan, Ozlem; Mozaffar, Tahseen; Pena, Loren D M; Simmons, Zachary; Straub, Volker; Young, Peter; Shafi, Raheel; Bjartmar, Carl; van der Ploeg, Ans

Thurberg, Beth L; Carlier, Pierre; Kissel, John T; Schoser, Benedikt; Pestronk, Alan; Barohn, Richard J; Goker-Alpan, Ozlem; Mozaffar, Tahseen; Pena, Loren D M; Simmons, Zachary; Straub, Volker; Young, Peter; Shafi, Raheel; Bjartmar, Carl; van der Ploeg, Ans.

Afiliación

Thurberg BL; Genzyme, a Sanofi Company, Cambridge, MA, USA.
Carlier P; Institut de Myologie, NMR Laboratory - Spectroscopy Laboratory, Université Pierre et Marie Curie, Paris, France.
Kissel JT; Department of Neurology, Division of Neuromuscular Medicine, Ohio State University Wexner Medical Center, Columbus, OH, USA.
Schoser B; Friedrich-Baur Institut, Neurologische Klinik, Klinikum der Universität München, Munich, Germany.
Pestronk A; Neuroscience Center, Center for Advanced Medicine, St. Louis, MO, USA.
Barohn RJ; Department of Neurology, University of Kansas Medical Center, Kansas City, KS, USA.
Goker-Alpan O; Lysosomal Disorders Unit and Center for Clinical Trials, O&O Alpan LLC, Fairfax, VA, USA.
Mozaffar T; Department of Neurology, University of California, Irvine, Irvine, CA, USA.
Pena LD; Division of Pediatric Medical Genetics, Duke University Medical Center, Durham, NC, USA.
Simmons Z; Penn State Hershey Neurology, Hershey, PA, USA.
Straub V; Institute of Genetic Medicine, Newcastle University, Newcastle upon Tyne, UK.
Young P; Department of Sleep Medicine and Neuromuscular Disorders, University Hospital of Münster, Münster, Germany.
Shafi R; Genzyme, a Sanofi Company, Cambridge, MA, USA.
Bjartmar C; Genzyme, a Sanofi Company, Cambridge, MA, USA.
van der Ploeg A; Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.

J Neuromuscul Dis ; 2(s1): S72-S73, 2015.

Article en En | MEDLINE | ID: mdl-27858658

Buscar en Google

Añadir a Mi BVS

Imprimir

XML

PubMed Links

Colección: 01-internacional Base de datos: MEDLINE Tipo de estudio: Observational_studies Idioma: En Revista: J Neuromuscul Dis Año: 2015 Tipo del documento: Article País de afiliación: Estados Unidos

Buscar en Google

Añadir a Mi BVS

Imprimir

XML

PubMed Links