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Structure-Based Designed Nano-Dysferlin Significantly Improves Dysferlinopathy in BLA/J Mice.
Llanga, Telmo; Nagy, Nadia; Conatser, Laura; Dial, Catherine; Sutton, R Bryan; Hirsch, Matthew L.
Afiliación
  • Llanga T; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA; Department of Ophthalmology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Nagy N; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA; Department of Ophthalmology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Conatser L; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA; Department of Ophthalmology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Dial C; Department of Ophthalmology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Sutton RB; Department of Cell Physiology and Molecular Biophysics, Texas Tech University Health Sciences Center, Lubbock, TX 79430, USA.
  • Hirsch ML; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA; Department of Ophthalmology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA. Electronic address: mhirsch@correspondence.unc.edu.
Mol Ther ; 25(9): 2150-2162, 2017 09 06.
Article en En | MEDLINE | ID: mdl-28629822

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Diseño de Fármacos / Distrofia Muscular de Cinturas / Disferlina Límite: Animals Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2017 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Diseño de Fármacos / Distrofia Muscular de Cinturas / Disferlina Límite: Animals Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2017 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos