Your browser doesn't support javascript.
loading
Prevention of Cholestatic Liver Disease and Reduced Tumorigenicity in a Murine Model of PFIC Type 3 Using Hybrid AAV-piggyBac Gene Therapy.
Siew, Susan M; Cunningham, Sharon C; Zhu, Erhua; Tay, Szun S; Venuti, Elena; Bolitho, Christine; Alexander, Ian E.
Afiliación
  • Siew SM; Department of Gastroenterology and James Fairfax Institute of Pediatric Nutrition, Sydney Children's Hospitals Network, Westmead, Australia.
  • Cunningham SC; Gene Therapy Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, The University of Sydney and Sydney Children's Hospitals Network, Westmead, Australia.
  • Zhu E; Gene Therapy Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, The University of Sydney and Sydney Children's Hospitals Network, Westmead, Australia.
  • Tay SS; Gene Therapy Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, The University of Sydney and Sydney Children's Hospitals Network, Westmead, Australia.
  • Venuti E; Gene Therapy Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, The University of Sydney and Sydney Children's Hospitals Network, Westmead, Australia.
  • Bolitho C; Department of Gastroenterology and James Fairfax Institute of Pediatric Nutrition, Sydney Children's Hospitals Network, Westmead, Australia.
  • Alexander IE; Gene Therapy Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, The University of Sydney and Sydney Children's Hospitals Network, Westmead, Australia.
Hepatology ; 70(6): 2047-2061, 2019 12.
Article en En | MEDLINE | ID: mdl-31099022

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Elementos Transponibles de ADN / Terapia Genética / Colestasis Intrahepática / Dependovirus / Subfamilia B de Transportador de Casetes de Unión a ATP / Neoplasias Hepáticas Experimentales Límite: Animals / Humans / Male Idioma: En Revista: Hepatology Año: 2019 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Elementos Transponibles de ADN / Terapia Genética / Colestasis Intrahepática / Dependovirus / Subfamilia B de Transportador de Casetes de Unión a ATP / Neoplasias Hepáticas Experimentales Límite: Animals / Humans / Male Idioma: En Revista: Hepatology Año: 2019 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Estados Unidos