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Antisense Oligonucleotide Reverses Leukodystrophy in Canavan Disease Mice.
Hull, Vanessa; Wang, Yan; Burns, Travis; Zhang, Sheng; Sternbach, Sarah; McDonough, Jennifer; Guo, Fuzheng; Pleasure, David.
Afiliación
  • Hull V; Institute for Pediatric Regenerative Medicine, University of California Davis School of Medicine and Shriners Hospitals for Children, Sacramento, CA.
  • Wang Y; Institute for Pediatric Regenerative Medicine, University of California Davis School of Medicine and Shriners Hospitals for Children, Sacramento, CA.
  • Burns T; Institute for Pediatric Regenerative Medicine, University of California Davis School of Medicine and Shriners Hospitals for Children, Sacramento, CA.
  • Zhang S; Institute for Pediatric Regenerative Medicine, University of California Davis School of Medicine and Shriners Hospitals for Children, Sacramento, CA.
  • Sternbach S; Department of Biological Sciences, Kent State University, Kent, OH.
  • McDonough J; Department of Biological Sciences, Kent State University, Kent, OH.
  • Guo F; Institute for Pediatric Regenerative Medicine, University of California Davis School of Medicine and Shriners Hospitals for Children, Sacramento, CA.
  • Pleasure D; Institute for Pediatric Regenerative Medicine, University of California Davis School of Medicine and Shriners Hospitals for Children, Sacramento, CA.
Ann Neurol ; 87(3): 480-485, 2020 03.
Article en En | MEDLINE | ID: mdl-31925837

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Oligonucleótidos Antisentido / Ácido Aspártico / Enfermedad de Canavan Límite: Animals Idioma: En Revista: Ann Neurol Año: 2020 Tipo del documento: Article País de afiliación: Canadá Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Oligonucleótidos Antisentido / Ácido Aspártico / Enfermedad de Canavan Límite: Animals Idioma: En Revista: Ann Neurol Año: 2020 Tipo del documento: Article País de afiliación: Canadá Pais de publicación: Estados Unidos