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Persistent repression of tau in the brain using engineered zinc finger protein transcription factors.
Wegmann, Susanne; DeVos, Sarah L; Zeitler, Bryan; Marlen, Kimberly; Bennett, Rachel E; Perez-Rando, Marta; MacKenzie, Danny; Yu, Qi; Commins, Caitlin; Bannon, Riley N; Corjuc, Bianca T; Chase, Alison; Diez, Lisa; Nguyen, Hoang-Oanh B; Hinkley, Sarah; Zhang, Lei; Goodwin, Alicia; Ledeboer, Annemarie; Lam, Stephen; Ankoudinova, Irina; Tran, Hung; Scarlott, Nicholas; Amora, Rainier; Surosky, Richard; Miller, Jeffrey C; Robbins, Ashley B; Rebar, Edward J; Urnov, Fyodor D; Holmes, Michael C; Pooler, Amy M; Riley, Brigit; Zhang, H Steve; Hyman, Bradley T.
Afiliación
  • Wegmann S; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA. bzeitler@sangamo.com susanne.wegmann@dzne.de bhyman@mgh.harvard.edu.
  • DeVos SL; German Center for Neurodegenerative Diseases (DZNE), 10117 Berlin, Germany.
  • Zeitler B; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Marlen K; Sangamo Therapeutics Inc., Richmond, CA 94804, USA. bzeitler@sangamo.com susanne.wegmann@dzne.de bhyman@mgh.harvard.edu.
  • Bennett RE; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Perez-Rando M; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • MacKenzie D; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Yu Q; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Commins C; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Bannon RN; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Corjuc BT; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Chase A; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Diez L; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Nguyen HB; German Center for Neurodegenerative Diseases (DZNE), 10117 Berlin, Germany.
  • Hinkley S; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Zhang L; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Goodwin A; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Ledeboer A; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Lam S; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Ankoudinova I; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Tran H; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Scarlott N; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Amora R; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Surosky R; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Miller JC; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Robbins AB; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Rebar EJ; Massachusetts General Hospital, Massachusetts Institute of Neurodegenerative Disease, Charlestown, MA 02129, USA.
  • Urnov FD; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Holmes MC; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Pooler AM; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Riley B; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Zhang HS; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
  • Hyman BT; Sangamo Therapeutics Inc., Richmond, CA 94804, USA.
Sci Adv ; 7(12)2021 03.
Article en En | MEDLINE | ID: mdl-33741591

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Factores de Transcripción / Enfermedad de Alzheimer Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Sci Adv Año: 2021 Tipo del documento: Article Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Factores de Transcripción / Enfermedad de Alzheimer Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Sci Adv Año: 2021 Tipo del documento: Article Pais de publicación: Estados Unidos