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Stepwise shortening of agalsidase beta infusion duration in Fabry disease: Clinical experience with infusion rate escalation protocol.
Riccio, Eleonora; Zanfardino, Mario; Franzese, Monica; Capuano, Ivana; Buonanno, Pasquale; Ferreri, Lucia; Amicone, Maria; Pisani, Antonio.
Afiliación
  • Riccio E; Institute for Biomedical Research and Innovation, National Research Council of Italy, Palermo, Italy.
  • Zanfardino M; IRCCS SDN, Naples, Italy.
  • Franzese M; IRCCS SDN, Naples, Italy.
  • Capuano I; Department of Public Health, Chair of Nephrology, University Federico II of Naples, Naples, Italy.
  • Buonanno P; Department of Neurosciences, Reproductive and Odontostomatological Sciences, University of Naples Federico II, Naples, Italy.
  • Ferreri L; Department of Public Health, Chair of Nephrology, University Federico II of Naples, Naples, Italy.
  • Amicone M; Department of Public Health, Chair of Nephrology, University Federico II of Naples, Naples, Italy.
  • Pisani A; Department of Public Health, Chair of Nephrology, University Federico II of Naples, Naples, Italy.
Mol Genet Genomic Med ; 9(5): e1659, 2021 05.
Article en En | MEDLINE | ID: mdl-33755336

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad de Fabry / Alfa-Galactosidasa / Terapia de Reemplazo Enzimático / Isoenzimas Tipo de estudio: Guideline / Observational_studies / Prognostic_studies Aspecto: Patient_preference Límite: Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Revista: Mol Genet Genomic Med Año: 2021 Tipo del documento: Article País de afiliación: Italia

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad de Fabry / Alfa-Galactosidasa / Terapia de Reemplazo Enzimático / Isoenzimas Tipo de estudio: Guideline / Observational_studies / Prognostic_studies Aspecto: Patient_preference Límite: Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Revista: Mol Genet Genomic Med Año: 2021 Tipo del documento: Article País de afiliación: Italia