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Categorizing hematological response to eculizumab in paroxysmal nocturnal hemoglobinuria: a multicenter real-life study.
Debureaux, Pierre-Edouard; Kulasekararaj, Austin G; Cacace, Fabiana; Silva, Bruno G P; Calado, Rodrigo T; Barone, Federica; Sicre de Fontbrune, Flore; Prata, Pedro Henrique; Soret, Juliette; Sica, Michela; Notaro, Rosario; Scheinberg, Phillip; Mallikarjuna, Vasundhara; Gandhi, Shreyans; Large, Joanna; Risitano, Antonio M; Peffault de Latour, Regis; Frieri, Camilla.
Afiliación
  • Debureaux PE; French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Saint-Louis hospital, Paris, France. pierre-edouard.debureaux@aphp.fr.
  • Kulasekararaj AG; Department of Hematological Medicine, King's College Hospital, National Institute of Health Research/Welcome King's Clinical Research Facility and King's College London, London, United Kingdom.
  • Cacace F; Severe Aplastic Anemia Working Party of the European Group for Blood and Marrow Transplantation, Leiden, the Netherlands.
  • Silva BGP; Federico II University of Naples, Department of Clinical Medicine and Surgery, Naples, Italy.
  • Calado RT; Department of Medical Imaging, Hematology, and Oncology, University of São Paulo, Ribeirão Preto, SP, Brazil.
  • Barone F; Department of Medical Imaging, Hematology, and Oncology, University of São Paulo, Ribeirão Preto, SP, Brazil.
  • Sicre de Fontbrune F; Laboratory of Cancer Genetics and Gene Transfer, Core Research Laboratory - Istituto per lo Studio, la Prevenzione e la Rete Oncologica (ISPRO), Florence, Italy.
  • Prata PH; Department of Hematology, University of Florence, Florence, Italy.
  • Soret J; French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Saint-Louis hospital, Paris, France.
  • Sica M; French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Saint-Louis hospital, Paris, France.
  • Notaro R; Department of Medical Imaging, Hematology, and Oncology, University of São Paulo, Ribeirão Preto, SP, Brazil.
  • Scheinberg P; University of Paris, Paris, France.
  • Mallikarjuna V; Clinical investigation center, Saint-Louis Hospital, Paris, France.
  • Gandhi S; Department of Hematology, University of Florence, Florence, Italy.
  • Large J; Laboratory of Cancer Genetics and Gene Transfer, Core Research Laboratory - Istituto per lo Studio, la Prevenzione e la Rete Oncologica (ISPRO), Florence, Italy.
  • Risitano AM; Division of Hematology, Hospital A Beneficência Portuguesa, Sao Paulo, Brazil.
  • Peffault de Latour R; Department of Hematological Medicine, King's College Hospital, National Institute of Health Research/Welcome King's Clinical Research Facility and King's College London, London, United Kingdom.
  • Frieri C; Department of Hematological Medicine, King's College Hospital, National Institute of Health Research/Welcome King's Clinical Research Facility and King's College London, London, United Kingdom.
Bone Marrow Transplant ; 56(10): 2600-2602, 2021 10.
Article en En | MEDLINE | ID: mdl-34226670

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Hemoglobinuria Paroxística Tipo de estudio: Clinical_trials Límite: Humans Idioma: En Revista: Bone Marrow Transplant Asunto de la revista: TRANSPLANTE Año: 2021 Tipo del documento: Article País de afiliación: Francia Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Hemoglobinuria Paroxística Tipo de estudio: Clinical_trials Límite: Humans Idioma: En Revista: Bone Marrow Transplant Asunto de la revista: TRANSPLANTE Año: 2021 Tipo del documento: Article País de afiliación: Francia Pais de publicación: Reino Unido