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Randomized Clinical Trial on the Long-Term Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1.
Hulton, Sally A; Groothoff, Jaap W; Frishberg, Yaacov; Koren, Michael J; Overcash, J Scott; Sellier-Leclerc, Anne-Laure; Shasha-Lavsky, Hadas; Saland, Jeffrey M; Hayes, Wesley; Magen, Daniella; Moochhala, Shabbir H; Coenen, Martin; Simkova, Eva; Garrelfs, Sander F; Sas, David J; Meliambro, Kristin A; Ngo, Taylor; Sweetser, Marianne T; Habtemariam, Bahru A; Gansner, John M; McGregor, Tracy L; Lieske, John C.
Afiliación
  • Hulton SA; Department of Nephrology, Birmingham Women's and Children's Hospital, Birmingham, UK.
  • Groothoff JW; Department of Pediatric Nephrology, Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.
  • Frishberg Y; Division of Pediatric Nephrology, Shaare Zedek Medical Center and Faculty of Medicine, Hebrew University of Jerusalem, Jerusalem, Israel.
  • Koren MJ; Jacksonville Center for Clinical Research, Jacksonville, Florida, USA.
  • Overcash JS; Velocity Clinical Research, San Diego, California, USA.
  • Sellier-Leclerc AL; Hôpital Femme Mère Enfant and Centre d'Investigation Clinique Institut National de la Santé et de la Recherche Médicale, Hospices Civils de Lyon, ERKnet, Bron, France.
  • Shasha-Lavsky H; Pediatric Nephrology Unit, Galilee Medical Center and Azrieli Faculty of Medicine, Bar-Ilan University, Nahariya, Israel.
  • Saland JM; Icahn School of Medicine at Mount Sinai, New York, New York, USA.
  • Hayes W; Department of Pediatric Nephrology, Great Ormond Street Hospital, London, UK.
  • Magen D; Pediatric Nephrology Institute, Rambam Health Care Campus, Haifa, Israel.
  • Moochhala SH; UCL Department of Renal Medicine, Royal Free Hospital, London, UK.
  • Coenen M; Department of Clinical Chemistry and Clinical Pharmacology, University Hospital Bonn, Bonn, Germany.
  • Simkova E; Al Jalila Children's Hospital, Dubai, United Arabs Emirates.
  • Garrelfs SF; Department of Pediatric Nephrology, Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.
  • Sas DJ; Division of Pediatric Nephrology and Hypertension, Mayo Clinic, Rochester, Minnesota, USA.
  • Meliambro KA; Icahn School of Medicine at Mount Sinai, New York, New York, USA.
  • Ngo T; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Sweetser MT; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Habtemariam BA; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Gansner JM; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • McGregor TL; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Lieske JC; Division of Nephrology and Hypertension, Mayo Clinic, Rochester, Minnesota, USA.
Kidney Int Rep ; 7(3): 494-506, 2022 Mar.
Article en En | MEDLINE | ID: mdl-35257062

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Tipo de estudio: Clinical_trials Idioma: En Revista: Kidney Int Rep Año: 2022 Tipo del documento: Article País de afiliación: Reino Unido Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Tipo de estudio: Clinical_trials Idioma: En Revista: Kidney Int Rep Año: 2022 Tipo del documento: Article País de afiliación: Reino Unido Pais de publicación: Estados Unidos