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Evaluation of Neurofilament Light Chain as a Biomarker of Neurodegeneration in X-Linked Childhood Cerebral Adrenoleukodystrophy.
Wang, Hongge; Davison, Matthew D; Kramer, Martin L; Qiu, Weiliang; Gladysheva, Tatiana; Chiang, Ruby M S; Kayatekin, Can; Nascene, David R; Taghizadeh, Leyla A; King, Carina J; Nolan, Erin E; Gupta, Ashish O; Orchard, Paul J; Lund, Troy C.
Afiliación
  • Wang H; Translational Sciences, Sanofi Research, Sanofi, Framingham, MA 01701, USA.
  • Davison MD; Translational Sciences, Sanofi Research, Sanofi, Framingham, MA 01701, USA.
  • Kramer ML; Translational Sciences, Sanofi Research, Sanofi, Framingham, MA 01701, USA.
  • Qiu W; Nonclinical Efficacy and Safety, Department of Biostatistics and Programming, Sanofi Development, Sanofi, Framingham, MA 01701, USA.
  • Gladysheva T; Integrated Drug Discovery, Sanofi Research, Sanofi, Waltham, MA 02451, USA.
  • Chiang RMS; Rare and Neurological Diseases Research Therapeutic Area, Sanofi, 49 New York Avenue, Framingham, MA 01701, USA.
  • Kayatekin C; Rare and Neurological Diseases Research Therapeutic Area, Sanofi, 49 New York Avenue, Framingham, MA 01701, USA.
  • Nascene DR; Department of Diagnostic Radiology, University of Minnesota Medical Center, Minneapolis, MN 55455, USA.
  • Taghizadeh LA; Division of Pediatric Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN 55455, USA.
  • King CJ; Division of Pediatric Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN 55455, USA.
  • Nolan EE; Division of Pediatric Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN 55455, USA.
  • Gupta AO; Division of Pediatric Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN 55455, USA.
  • Orchard PJ; Division of Pediatric Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN 55455, USA.
  • Lund TC; Division of Pediatric Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN 55455, USA.
Cells ; 11(5)2022 03 07.
Article en En | MEDLINE | ID: mdl-35269535

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Adrenoleucodistrofia Tipo de estudio: Diagnostic_studies Límite: Child / Humans / Male País/Región como asunto: Europa Idioma: En Revista: Cells Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Adrenoleucodistrofia Tipo de estudio: Diagnostic_studies Límite: Child / Humans / Male País/Región como asunto: Europa Idioma: En Revista: Cells Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos