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RNA-targeting and gene editing therapies for transthyretin amyloidosis.
Aimo, Alberto; Castiglione, Vincenzo; Rapezzi, Claudio; Franzini, Maria; Panichella, Giorgia; Vergaro, Giuseppe; Gillmore, Julian; Fontana, Marianna; Passino, Claudio; Emdin, Michele.
Afiliación
  • Aimo A; Institute of Life Sciences, Scuola Superiore Sant'Anna, Pisa, Italy. a.aimo@santannapisa.it.
  • Castiglione V; Cardiology Division, Fondazione Toscana Gabriele Monasterio, Pisa, Italy. a.aimo@santannapisa.it.
  • Rapezzi C; Institute of Life Sciences, Scuola Superiore Sant'Anna, Pisa, Italy.
  • Franzini M; Cardiologic Centre, University of Ferrara, Ferrara, Italy.
  • Panichella G; Maria Cecilia Hospital, GVM Care & Research, Cotignola (Ravenna), Italy.
  • Vergaro G; Department of Translational Research and New Technologies in Medicine and Surgery, University Hospital of Pisa, Pisa, Italy.
  • Gillmore J; Institute of Life Sciences, Scuola Superiore Sant'Anna, Pisa, Italy.
  • Fontana M; Institute of Life Sciences, Scuola Superiore Sant'Anna, Pisa, Italy.
  • Passino C; Cardiology Division, Fondazione Toscana Gabriele Monasterio, Pisa, Italy.
  • Emdin M; National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Hospital, London, UK.
Nat Rev Cardiol ; 19(10): 655-667, 2022 10.
Article en En | MEDLINE | ID: mdl-35322226

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Polineuropatías / Neuropatías Amiloides Familiares / Cardiomiopatías Límite: Humans Idioma: En Revista: Nat Rev Cardiol Asunto de la revista: CARDIOLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Italia Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Polineuropatías / Neuropatías Amiloides Familiares / Cardiomiopatías Límite: Humans Idioma: En Revista: Nat Rev Cardiol Asunto de la revista: CARDIOLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Italia Pais de publicación: Reino Unido