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Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia.
Ward, Leanne M; Glorieux, Francis H; Whyte, Michael P; Munns, Craig F; Portale, Anthony A; Högler, Wolfgang; Simmons, Jill H; Gottesman, Gary S; Padidela, Raja; Namba, Noriyuki; Cheong, Hae Il; Nilsson, Ola; Mao, Meng; Chen, Angel; Skrinar, Alison; Roberts, Mary Scott; Imel, Erik A.
Afiliación
  • Ward LM; Department of Pediatrics, Faculty of Medicine, University of Ottawa, Ottawa, Ontario K1H 8L1, Canada.
  • Glorieux FH; Shriners Hospitals for Children, Canada, McGill University, Montreal, Quebec H4A OA9, Canada.
  • Whyte MP; Shriners Hospitals for Children St Louis, St Louis, Missouri 63110,USA.
  • Munns CF; Child Health Research Centre, The University of Queensland, Brisbane, Queensland 4072, Australia.
  • Portale AA; Department of Endocrinology and Diabetes, Queensland Children's Hospital, Brisbane, Queensland 4101, Australia.
  • Högler W; Department of Pediatrics, University of California, San Francisco, San Francisco, California 94143, USA.
  • Simmons JH; Department of Pediatrics and Adolescent Medicine, Johannes Kepler University Linz, Linz 4040, Austria.
  • Gottesman GS; Institute of Metabolism and Systems Research, University of Birmingham, Birmingham, B15 2TT, UK.
  • Padidela R; Department of Pediatrics, Division of Endocrinology and Diabetes, Vanderbilt University School of Medicine, Vanderbilt University, 680-8570 Nashville, Tennessee, 63110, USA.
  • Namba N; Shriners Hospitals for Children St Louis, St Louis, Missouri 63110, USA.
  • Cheong HI; Department of Paediatric Endocrinology, Royal Manchester Children's Hospital, Manchester M13 9WL, UK.
  • Nilsson O; Department of Pediatrics, Osaka Hospital, Japan.
  • Mao M; Community Healthcare Organization.
  • Chen A; Osaka University Graduate School of Medicine, Osaka 553-0003, Japan.
  • Skrinar A; Division of Pediatrics and Perinatology, Tottori University Faculty of Medicine, Yonago, Japan.
  • Roberts MS; Department of Pediatrics, Seoul National University Children's Hospital, Seoul 14068, South Korea.
  • Imel EA; Division of Pediatric Endocrinology and Center for Molecular Medicine, Karolinska Institutet, Stockholm 17177, Sweden.
J Clin Endocrinol Metab ; 107(8): e3241-e3253, 2022 07 14.
Article en En | MEDLINE | ID: mdl-35533340

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Hipofosfatemia / Raquitismo Hipofosfatémico Familiar Tipo de estudio: Clinical_trials / Guideline Límite: Adolescent / Child / Humans Idioma: En Revista: J Clin Endocrinol Metab Año: 2022 Tipo del documento: Article País de afiliación: Canadá Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Hipofosfatemia / Raquitismo Hipofosfatémico Familiar Tipo de estudio: Clinical_trials / Guideline Límite: Adolescent / Child / Humans Idioma: En Revista: J Clin Endocrinol Metab Año: 2022 Tipo del documento: Article País de afiliación: Canadá Pais de publicación: Estados Unidos