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Improving Gene Therapy for Angelman Syndrome with Secreted Human UBE3A.
Nenninger, Austin W; Willman, Matthew; Willman, Jonathan; Stewart, Emma; Mesidor, Philippe; Novoa, Michelle; Morrill, Nicole K; Alvarez, Luis; Joly-Amado, Aurélie; Peters, Melinda M; Gulick, Danielle; Nash, Kevin R.
Afiliación
  • Nenninger AW; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Willman M; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Willman J; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Stewart E; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Mesidor P; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Novoa M; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Morrill NK; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Alvarez L; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Joly-Amado A; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Peters MM; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Gulick D; Department of Molecular Pharmacology and Physiology, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
  • Nash KR; Department of Molecular Medicine, Morsani College of Medicine, University of South Florida, 12901 Bruce B Downs Blvd, Tampa, FL-33612, USA.
Neurotherapeutics ; 19(4): 1329-1339, 2022 07.
Article en En | MEDLINE | ID: mdl-35534672

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Síndrome de Angelman / Ubiquitina-Proteína Ligasas / Péptidos de Penetración Celular Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Neurotherapeutics Asunto de la revista: NEUROLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Síndrome de Angelman / Ubiquitina-Proteína Ligasas / Péptidos de Penetración Celular Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Neurotherapeutics Asunto de la revista: NEUROLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos