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Rectal organoid-guided CFTR modulator therapy restores lung function in a cystic fibrosis patient with the rare 1677delTA/R334W genotype.
Mitropoulou, Georgia; Brandenberg, Nathalie; Hoehnel, Sylke; Ceroni, Camilla; Balmpouzis, Zisis; Blanchon, Sylvain; Dorta, Gian; Sauty, Alain; Koutsokera, Angela.
Afiliación
  • Mitropoulou G; Adult Cystic Fibrosis and CFTR-related disorders Center, Division of Pulmonology, Dept of Medicine, Lausanne University Hospital and University of Lausanne, Lausanne, Switzerland georgia.mitropoulou@chuv.ch.
  • Brandenberg N; Lung Transplant Center, Division of Pulmonology, Dept of Medicine, Lausanne University Hospital and University of Lausanne, Lausanne, Switzerland.
  • Hoehnel S; Laboratory of Stem Cell Bioengineering, Institute of Bioengineering, School of Life Sciences, Swiss Federal Institute of Technology, Lausanne, Switzerland.
  • Ceroni C; SUN bioscience, EPFL Innovation Park, Lausanne, Switzerland.
  • Balmpouzis Z; Laboratory of Stem Cell Bioengineering, Institute of Bioengineering, School of Life Sciences, Swiss Federal Institute of Technology, Lausanne, Switzerland.
  • Blanchon S; SUN bioscience, EPFL Innovation Park, Lausanne, Switzerland.
  • Dorta G; Laboratory of Stem Cell Bioengineering, Institute of Bioengineering, School of Life Sciences, Swiss Federal Institute of Technology, Lausanne, Switzerland.
  • Sauty A; SUN bioscience, EPFL Innovation Park, Lausanne, Switzerland.
  • Koutsokera A; Adult Cystic Fibrosis and CFTR-related disorders Center, Division of Pulmonology, Dept of Medicine, Lausanne University Hospital and University of Lausanne, Lausanne, Switzerland.
Eur Respir J ; 60(6)2022 12.
Article en En | MEDLINE | ID: mdl-36423906

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Fibrosis Quística Límite: Humans Idioma: En Revista: Eur Respir J Año: 2022 Tipo del documento: Article País de afiliación: Suiza

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Fibrosis Quística Límite: Humans Idioma: En Revista: Eur Respir J Año: 2022 Tipo del documento: Article País de afiliación: Suiza
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