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Myelodysplasia after clonal hematopoiesis with APOBEC3-mediated CYBB inactivation in retroviral gene therapy for X-CGD.
Uchiyama, Toru; Kawai, Toshinao; Nakabayashi, Kazuhiko; Nakazawa, Yumiko; Goto, Fumihiro; Okamura, Kohji; Nishimura, Toyoki; Kato, Koji; Watanabe, Nobuyuki; Miura, Akane; Yasuda, Toru; Ando, Yukiko; Minegishi, Tomoko; Edasawa, Kaori; Shimura, Marika; Akiba, Yumi; Sato-Otsubo, Aiko; Mizukami, Tomoyuki; Kato, Motohiro; Akashi, Koichi; Nunoi, Hiroyuki; Onodera, Masafumi.
Afiliación
  • Uchiyama T; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan. Electronic address: uchiyama-t@ncchd.go.jp.
  • Kawai T; Division of Immunology, National Center for Child Health and Development, Tokyo, Japan.
  • Nakabayashi K; Department of Maternal-Fetal Biology, National Center for Child Health and Development, Tokyo, Japan.
  • Nakazawa Y; Division of Immunology, National Center for Child Health and Development, Tokyo, Japan.
  • Goto F; Division of Immunology, National Center for Child Health and Development, Tokyo, Japan.
  • Okamura K; Department of Systems BioMedicine, National Center for Child Health and Development, Tokyo, Japan.
  • Nishimura T; Division of Pediatrics, Faculty of Medicine, University of Miyazaki, Miyazaki, Japan.
  • Kato K; Department of Medicine and Biosystemic Science, Kyushu University Graduate School of Medical Science, Fukuoka, Japan.
  • Watanabe N; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Miura A; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Yasuda T; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Ando Y; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Minegishi T; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Edasawa K; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Shimura M; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Akiba Y; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
  • Sato-Otsubo A; Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan; Pediatric Hematology and Oncology, National Center for Child Health and Development, Tokyo, Japan.
  • Mizukami T; Department of Pediatrics, NHO Kumamoto Medical Center, Kumamoto, Japan.
  • Kato M; Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan; Pediatric Hematology and Oncology, National Center for Child Health and Development, Tokyo, Japan.
  • Akashi K; Department of Medicine and Biosystemic Science, Kyushu University Graduate School of Medical Science, Fukuoka, Japan.
  • Nunoi H; Division of Pediatrics, Faculty of Medicine, University of Miyazaki, Miyazaki, Japan.
  • Onodera M; Department of Human Genetics, National Center for Child Health and Development, Tokyo, Japan.
Mol Ther ; 31(12): 3424-3440, 2023 Dec 06.
Article en En | MEDLINE | ID: mdl-37705244

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Síndromes Mielodisplásicos / Enfermedad Granulomatosa Crónica Límite: Adult / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2023 Tipo del documento: Article Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Síndromes Mielodisplásicos / Enfermedad Granulomatosa Crónica Límite: Adult / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2023 Tipo del documento: Article Pais de publicación: Estados Unidos