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Efficacy, safety and cost of emicizumab prophylaxis in haemophilia A patients with inhibitors: A nationwide observational study in Taiwan.
Shen, Ming-Ching; Chou, Sheng-Chieh; Chiou, Shyh-Shin; Lin, Pei-Chin; Chen, Yeu-Chin; Lin, Hsuan-Yu; Lee, Yang-Cheng; Huang, Cih-En; Weng, Te-Fu; Huang, Ting-Huan; Chung, Chih-Yuan; Chen, Jiann-Shiuh; Chen, Shu-Huey; Cheng, Shin-Nan; Hsiao, Chih-Cheng; Huang, Yen-Min; Chen, Shih-Hsiang; Yu, Yuan-Bin; Lin, Shih-Chiang; Lin, Ching-Yeh; Peng, Ching-Tien; Wang, Jiaan-Der.
Afiliación
  • Shen MC; Department of Internal Medicine, Changhua Christian Hospital, Changhua, Taiwan.
  • Chou SC; Division of Hematology, Department of Internal Medicine, National Taiwan University Hospital, Taipei, Taiwan.
  • Chiou SS; Division of Hematology, Department of Internal Medicine, National Taiwan University Hospital, Taipei, Taiwan.
  • Lin PC; Department of Pediatrics, School of Medicine, College of Medicine, Kaohsiung Medical University, Kaohsiung, Taiwan.
  • Chen YC; Division of Hematology and Oncology, Department of Pediatrics, Kaohsiung Medical University Hospital, Kaohsiung, Taiwan.
  • Lin HY; Department of Pediatrics, School of Medicine, College of Medicine, Kaohsiung Medical University, Kaohsiung, Taiwan.
  • Lee YC; Division of Hematology and Oncology, Department of Pediatrics, Kaohsiung Medical University Hospital, Kaohsiung, Taiwan.
  • Huang CE; Hemophilia Care and Research Center, Tri-Service General Hospital, Taipei, Taiwan.
  • Weng TF; Division of Hematology/Oncology, Department of Internal Medicine, Tri-Service General Hospital, National Defense Medical Center, Taipei, Taiwan.
  • Huang TH; Department of Internal Medicine, Changhua Christian Hospital, Changhua, Taiwan.
  • Chung CY; Division of Hematology and Oncology, Departments of Internal Medicine, Tainan Municipal Hospital, Tainan, Taiwan.
  • Chen JS; Division of Hematology and Oncology, Department of Medicine, Chang Gung Memorial Hospital at Chiayi, Chiayi, Taiwan.
  • Chen SH; Division of Pediatric Hematology/Oncology, Department of Pediatrics, Chung Shan Medical University Hospital, Taichung, Taiwan.
  • Cheng SN; Division of Pediatric Hematology/Oncology, Hsinchu Mackay Memorial Hospital, Hsinchu, Taiwan.
  • Hsiao CC; Department of Medical Oncology, China Medical University Hsinchu Hospital, Hsinchu, Taiwan.
  • Huang YM; Division of Hematology and Oncology, Department of Pediatrics, National Cheng Kung University Hospital, Tainan, Taiwan.
  • Chen SH; Department of Pediatrics, Shuang Ho Hospital, Ministry of Health and Welfare, Taipei Medical University, New Taipei, Taiwan.
  • Yu YB; Department of Pediatrics, School of Medicine, College of Medicine, Taipei Medical University, Taipei, Taiwan.
  • Lin SC; Haemophilia Care and Research Center, Tri-Service General Hospital, School of Medicine, National Defense Medical Center, Taipei, Taiwan.
  • Lin CY; Department of Paediatrics, Tung's Taichung Metrohabor Hospital, Taichung, Taiwan.
  • Peng CT; Division of Pediatric Hematology/Oncology, Kaohsiung Chang Gung Memorial Hospital, Kaohsiung, Taiwan.
  • Wang JD; Division of Hematology and Oncology, Department of Internal Medicine, Hemophilia and Thrombosis Treatment Center, Chang Gung Memorial Hospital, Keelung, Taiwan.
Haemophilia ; 29(6): 1499-1508, 2023 Nov.
Article en En | MEDLINE | ID: mdl-37819166

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Anticuerpos Biespecíficos / Hemofilia A Tipo de estudio: Health_economic_evaluation / Observational_studies Límite: Adult / Humans País/Región como asunto: Asia Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2023 Tipo del documento: Article País de afiliación: Taiwán Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Anticuerpos Biespecíficos / Hemofilia A Tipo de estudio: Health_economic_evaluation / Observational_studies Límite: Adult / Humans País/Región como asunto: Asia Idioma: En Revista: Haemophilia Asunto de la revista: HEMATOLOGIA Año: 2023 Tipo del documento: Article País de afiliación: Taiwán Pais de publicación: Reino Unido