Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations.

Brown, Sharon J; Yáñez-Muñoz, Rafael J; Fuller, Heidi R

Brown, Sharon J; Yáñez-Muñoz, Rafael J; Fuller, Heidi R.

Afiliación

Brown SJ; School of Pharmacy and Bioengineering, Keele University, Keele, UK (Brown SJ, Fuller HR).
Yáñez-Muñoz RJ; Wolfson Center for Inherited Neuromuscular Disease, TORCH Building, RJAH Orthopaedic Hospital, Oswestry, UK (Brown SJ, Fuller HR).
Fuller HR; AGCTlab.org, Center of Gene and Cell Therapy, Department of Biological Sciences, School of Life Sciences and the Environment, Royal Holloway University of London, Egham, UK (Yáñez-Muñoz RJ).

Neural Regen Res ; 20(7): 2011-2012, 2025 Jul 01.

Article en En | MEDLINE | ID: mdl-39254562

Texto completo

Añadir a Mi BVS

Imprimir

XML

PubMed Links

Buscar en Google

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Neural Regen Res Año: 2025 Tipo del documento: Article Pais de publicación: India

Texto completo

Añadir a Mi BVS

Imprimir

XML

PubMed Links

Buscar en Google