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2'-O-Methyl RNA/Ethylene-Bridged Nucleic Acid Chimera Antisense Oligonucleotides to Induce Dystrophin Exon 45 Skipping.
Lee, Tomoko; Awano, Hiroyuki; Yagi, Mariko; Matsumoto, Masaaki; Watanabe, Nobuaki; Goda, Ryoya; Koizumi, Makoto; Takeshima, Yasuhiro; Matsuo, Masafumi.
Affiliation
  • Lee T; Department of Pediatrics, Hyogo College of Medicine, Nishinomiya 6638501, Japan. leeleetomo@me.com.
  • Awano H; Department of Pediatrics, Kobe University Graduate School of Medicine, Kobe 6500017, Japan. awahiro@med.kobe-u.ac.jp.
  • Yagi M; Nikoniko House Medical and Welfare Center, Kobe 6511102, Japan. marikoyagi.sgt@gmail.com.
  • Matsumoto M; Department of Pediatrics, Kobe University Graduate School of Medicine, Kobe 6500017, Japan. mmatsu@med.kobe-u.ac.jp.
  • Watanabe N; Drug Metabolism & Pharmacokinetics Research Laboratories, Daiichi Sankyo Co., Ltd., Tokyo 1408710, Japan. watanabe.nobuaki.nc@daiichisankyo.co.jp.
  • Goda R; Drug Metabolism & Pharmacokinetics Research Laboratories, Daiichi Sankyo Co., Ltd., Tokyo 1408710, Japan. goda.ryoya.u4@daiichisankyo.co.jp.
  • Koizumi M; Modality Research Laboratories, Daiichi Sankyo Co., Ltd., Tokyo 1408710, Japan. koizumi.makoto.h7@daiichisankyo.co.jp.
  • Takeshima Y; Department of Pediatrics, Hyogo College of Medicine, Nishinomiya 6638501, Japan. ytake@hyo-med.ac.jp.
  • Matsuo M; Department of Physical Therapy, Faculty of Rehabilitation, Kobe Gakuin University, Kobe 6512180, Japan. mmatsuo@reha.kobegakuin.ac.jp.
Genes (Basel) ; 8(2)2017 Feb 10.
Article in En | MEDLINE | ID: mdl-28208626

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Genes (Basel) Year: 2017 Document type: Article Affiliation country:

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Genes (Basel) Year: 2017 Document type: Article Affiliation country: