Fine-tuned cholesterol solubilizer, mono-6-O-α-D-maltosyl-γ-cyclodextrin, ameliorates experimental Niemann-Pick disease type C without hearing loss.
Biomed Pharmacother
; 155: 113698, 2022 Nov.
Article
in En
| MEDLINE
| ID: mdl-36116252
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Gamma-Cyclodextrins
/
Niemann-Pick Disease, Type C
/
Ototoxicity
/
Hearing Loss
Type of study:
Prognostic_studies
Limits:
Animals
Language:
En
Journal:
Biomed Pharmacother
Year:
2022
Document type:
Article
Country of publication: