Enzyme replacement therapy with laronidase (Aldurazyme(®)) for treating mucopolysaccharidosis type I.
Cochrane Database Syst Rev
; (11): CD009354, 2013 Nov 21.
Article
de En
| MEDLINE
| ID: mdl-24257962
Texte intégral:
1
Collection:
01-internacional
Base de données:
MEDLINE
Sujet principal:
Mucopolysaccharidose de type I
/
Maladies rares
/
Thérapie enzymatique substitutive
/
L-iduronidase
Type d'étude:
Clinical_trials
/
Prognostic_studies
/
Systematic_reviews
Aspects:
Patient_preference
Limites:
Adolescent
/
Adult
/
Child
/
Female
/
Humans
/
Male
Langue:
En
Journal:
Cochrane Database Syst Rev
Sujet du journal:
PESQUISA EM SERVICOS DE SAUDE
Année:
2013
Type de document:
Article
Pays de publication:
Royaume-Uni