Safety, pharmacokinetics, and preliminary assessment of efficacy of mecasermin (recombinant human IGF-1) for the treatment of Rett syndrome.

Khwaja, Omar S; Ho, Eugenia; Barnes, Katherine V; O'Leary, Heather M; Pereira, Luis M; Finkelstein, Yaron; Nelson, Charles A; Vogel-Farley, Vanessa; DeGregorio, Geneva; Holm, Ingrid A; Khatwa, Umakanth; Kapur, Kush; Alexander, Mark E; Finnegan, Deirdre M; Cantwell, Nicole G; Walco, Alexandra C; Rappaport, Leonard; Gregas, Matt; Fichorova, Raina N; Shannon, Michael W; Sur, Mriganka; Kaufmann, Walter E

Khwaja, Omar S; Ho, Eugenia; Barnes, Katherine V; O'Leary, Heather M; Pereira, Luis M; Finkelstein, Yaron; Nelson, Charles A; Vogel-Farley, Vanessa; DeGregorio, Geneva; Holm, Ingrid A; Khatwa, Umakanth; Kapur, Kush; Alexander, Mark E; Finnegan, Deirdre M; Cantwell, Nicole G; Walco, Alexandra C; Rappaport, Leonard; Gregas, Matt; Fichorova, Raina N; Shannon, Michael W; Sur, Mriganka; Kaufmann, Walter E.

Affiliation

Khwaja OS; Department of Neurology, Boston Children's Hospital and Harvard Medical School, Boston, MA 02115.

Proc Natl Acad Sci U S A ; 111(12): 4596-601, 2014 Mar 25.

Article de En | MEDLINE | ID: mdl-24623853

Sujet(s)

Texte intégral

Ajouter à My VHL

Imprimer

XML

PubMed Links

Recherche sur Google

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Facteur de croissance IGF-I / Syndrome de Rett / Protéines et peptides de signalisation intercellulaire Type d'étude: Prognostic_studies Limites: Child / Child, preschool / Female / Humans Langue: En Journal: Proc Natl Acad Sci U S A Année: 2014 Type de document: Article Pays de publication: États-Unis d'Amérique

Texte intégral

Ajouter à My VHL

Imprimer

XML

PubMed Links

Recherche sur Google